A randomized, phase 2 clinical trial of lithium carbonate in Machado-Joseph disease.
Identifieur interne : 000681 ( Main/Curation ); précédent : 000680; suivant : 000682A randomized, phase 2 clinical trial of lithium carbonate in Machado-Joseph disease.
Auteurs : Jonas Alex Morales Saute [Brésil] ; Raphael Machado De Castilhos ; Thais Lampert Monte ; Artur Francisco Schumacher-Schuh ; Karina Carvalho Donis ; Rui D'Ávila ; Gabriele Nunes Souza ; Aline Dutra Russo ; Gabriel Vasata Furtado ; Tailise Conte Gheno ; Diogo Onofre Gomes De Souza ; Luis Valmor Cruz Portela ; Maria-Luiza Saraiva-Pereira ; Suzi Alvez Camey ; Vanessa Bielefeld Leotti Torman ; Carlos Roberto De Mello Rieder ; Laura Bannach JardimSource :
- Movement disorders : official journal of the Movement Disorder Society [ 1531-8257 ] ; 2014.
English descriptors
- KwdEn :
- MESH :
- chemical , adverse effects : Enzyme Inhibitors, Lithium Carbonate.
- chemical , therapeutic use : Enzyme Inhibitors, Lithium Carbonate.
- drug therapy : Machado-Joseph Disease.
- Adult, Double-Blind Method, Female, Humans, Male, Middle Aged, Treatment Outcome.
Abstract
Because lithium exerts neuroprotective effects in preclinical models of polyglutamine disorders, our objective was to assess the safety and efficacy of lithium carbonate (0.5-0.8 milliequivalents per liter) in patients with Machado-Joseph disease (spinocerebellar ataxia type 3 [MJD/SCA3]).
DOI: 10.1002/mds.25803
PubMed: 24399647
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pubmed:24399647Le document en format XML
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<author><name sortKey="Saute, Jonas Alex Morales" sort="Saute, Jonas Alex Morales" uniqKey="Saute J" first="Jonas Alex Morales" last="Saute">Jonas Alex Morales Saute</name>
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<author><name sortKey="Saraiva Pereira, Maria Luiza" sort="Saraiva Pereira, Maria Luiza" uniqKey="Saraiva Pereira M" first="Maria-Luiza" last="Saraiva-Pereira">Maria-Luiza Saraiva-Pereira</name>
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<sourceDesc><biblStruct><analytic><title xml:lang="en">A randomized, phase 2 clinical trial of lithium carbonate in Machado-Joseph disease.</title>
<author><name sortKey="Saute, Jonas Alex Morales" sort="Saute, Jonas Alex Morales" uniqKey="Saute J" first="Jonas Alex Morales" last="Saute">Jonas Alex Morales Saute</name>
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<author><name sortKey="De Castilhos, Raphael Machado" sort="De Castilhos, Raphael Machado" uniqKey="De Castilhos R" first="Raphael Machado" last="De Castilhos">Raphael Machado De Castilhos</name>
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<author><name sortKey="Schumacher Schuh, Artur Francisco" sort="Schumacher Schuh, Artur Francisco" uniqKey="Schumacher Schuh A" first="Artur Francisco" last="Schumacher-Schuh">Artur Francisco Schumacher-Schuh</name>
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<author><name sortKey="Gheno, Tailise Conte" sort="Gheno, Tailise Conte" uniqKey="Gheno T" first="Tailise Conte" last="Gheno">Tailise Conte Gheno</name>
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<author><name sortKey="Saraiva Pereira, Maria Luiza" sort="Saraiva Pereira, Maria Luiza" uniqKey="Saraiva Pereira M" first="Maria-Luiza" last="Saraiva-Pereira">Maria-Luiza Saraiva-Pereira</name>
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<author><name sortKey="Torman, Vanessa Bielefeld Leotti" sort="Torman, Vanessa Bielefeld Leotti" uniqKey="Torman V" first="Vanessa Bielefeld Leotti" last="Torman">Vanessa Bielefeld Leotti Torman</name>
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<author><name sortKey="De Mello Rieder, Carlos Roberto" sort="De Mello Rieder, Carlos Roberto" uniqKey="De Mello Rieder C" first="Carlos Roberto" last="De Mello Rieder">Carlos Roberto De Mello Rieder</name>
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<series><title level="j">Movement disorders : official journal of the Movement Disorder Society</title>
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<term>Double-Blind Method</term>
<term>Enzyme Inhibitors (adverse effects)</term>
<term>Enzyme Inhibitors (therapeutic use)</term>
<term>Female</term>
<term>Humans</term>
<term>Lithium Carbonate (adverse effects)</term>
<term>Lithium Carbonate (therapeutic use)</term>
<term>Machado-Joseph Disease (drug therapy)</term>
<term>Male</term>
<term>Middle Aged</term>
<term>Treatment Outcome</term>
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<term>Lithium Carbonate</term>
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<keywords scheme="MESH" type="chemical" qualifier="therapeutic use" xml:lang="en"><term>Enzyme Inhibitors</term>
<term>Lithium Carbonate</term>
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<keywords scheme="MESH" qualifier="drug therapy" xml:lang="en"><term>Machado-Joseph Disease</term>
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<keywords scheme="MESH" xml:lang="en"><term>Adult</term>
<term>Double-Blind Method</term>
<term>Female</term>
<term>Humans</term>
<term>Male</term>
<term>Middle Aged</term>
<term>Treatment Outcome</term>
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<front><div type="abstract" xml:lang="en">Because lithium exerts neuroprotective effects in preclinical models of polyglutamine disorders, our objective was to assess the safety and efficacy of lithium carbonate (0.5-0.8 milliequivalents per liter) in patients with Machado-Joseph disease (spinocerebellar ataxia type 3 [MJD/SCA3]).</div>
</front>
</TEI>
</record>
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