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<record><TEI><teiHeader><fileDesc><titleStmt><title xml:lang="en">Erratum to: An exploratory randomised double-blind and placebo-controlled phase 2 study of a combination of baclofen, naltrexone and sorbitol (PXT3003) in patients with Charcot-Marie-Tooth disease type 1A</title><author><name sortKey="Attarian, Shahram" sort="Attarian, Shahram" uniqKey="Attarian S" first="Shahram" last="Attarian">Shahram Attarian</name><affiliation><nlm:aff id="Aff1">Centre de référence des maladies neuromusculaires et de la SLA, Pôle des neurosciences Cliniques, AP-HM et Aix Marseille Université, Marseille, France</nlm:aff></affiliation></author><author><name sortKey="Vallat, Jean Michel" sort="Vallat, Jean Michel" uniqKey="Vallat J" first="Jean-Michel" last="Vallat">Jean-Michel Vallat</name><affiliation><nlm:aff id="Aff3">CHU de Limoges - Hôpital Dupuytren, 2 Avenue Martin Luther King, 87042 Limoges, France</nlm:aff></affiliation></author><author><name sortKey="Magy, Laurent" sort="Magy, Laurent" uniqKey="Magy L" first="Laurent" last="Magy">Laurent Magy</name><affiliation><nlm:aff id="Aff3">CHU de Limoges - Hôpital Dupuytren, 2 Avenue Martin Luther King, 87042 Limoges, France</nlm:aff></affiliation></author><author><name sortKey="Funalot, Benoit" sort="Funalot, Benoit" uniqKey="Funalot B" first="Benoît" last="Funalot">Benoît Funalot</name><affiliation><nlm:aff id="Aff3">CHU de Limoges - Hôpital Dupuytren, 2 Avenue Martin Luther King, 87042 Limoges, France</nlm:aff></affiliation></author><author><name sortKey="Gonnaud, Pierre Marie" sort="Gonnaud, Pierre Marie" uniqKey="Gonnaud P" first="Pierre-Marie" last="Gonnaud">Pierre-Marie Gonnaud</name><affiliation><nlm:aff id="Aff4">CHU Lyon Sud, 165 Chemin du Grand Revoyet, 69495 Lyon, France</nlm:aff></affiliation></author><author><name sortKey="Lacour, Arnaud" sort="Lacour, Arnaud" uniqKey="Lacour A" first="Arnaud" last="Lacour">Arnaud Lacour</name><affiliation><nlm:aff id="Aff5">CHRU de Lille - Hôpital Roger Salengro, rue Emile Laine, 59037 Lille, France</nlm:aff></affiliation></author><author><name sortKey="Pereon, Yann" sort="Pereon, Yann" uniqKey="Pereon Y" first="Yann" last="Péréon">Yann Péréon</name><affiliation><nlm:aff id="Aff6">CHU de Nantes - Hôtel Dieu, 1 place Alexis Ricordeau, 44093 Nantes, France</nlm:aff></affiliation></author><author><name sortKey="Dubourg, Odile" sort="Dubourg, Odile" uniqKey="Dubourg O" first="Odile" last="Dubourg">Odile Dubourg</name><affiliation><nlm:aff id="Aff7">CHU de Paris - Groupe Hospitalier Pitié-Salpétrière, 47-83 boulevard de l’Hôpital, 75013 Paris, France</nlm:aff></affiliation></author><author><name sortKey="Pouget, Jean" sort="Pouget, Jean" uniqKey="Pouget J" first="Jean" last="Pouget">Jean Pouget</name><affiliation><nlm:aff id="Aff1">Centre de référence des maladies neuromusculaires et de la SLA, Pôle des neurosciences Cliniques, AP-HM et Aix Marseille Université, Marseille, France</nlm:aff></affiliation></author><author><name sortKey="Micallef, Joelle" sort="Micallef, Joelle" uniqKey="Micallef J" first="Joëlle" last="Micallef">Joëlle Micallef</name><affiliation><nlm:aff id="Aff2">CIC-Centre de Pharmacologie Clinique et D’Evaluations Therapeutiques, AP-HM et Aix Marseille Université, Marseille, France</nlm:aff></affiliation></author><author><name sortKey="Franques, Jerome" sort="Franques, Jerome" uniqKey="Franques J" first="Jérôme" last="Franques">Jérôme Franques</name><affiliation><nlm:aff id="Aff1">Centre de référence des maladies neuromusculaires et de la SLA, Pôle des neurosciences Cliniques, AP-HM et Aix Marseille Université, Marseille, France</nlm:aff></affiliation></author><author><name sortKey="Lefebvre, Marie Noelle" sort="Lefebvre, Marie Noelle" uniqKey="Lefebvre M" first="Marie-Noëlle" last="Lefebvre">Marie-Noëlle Lefebvre</name><affiliation><nlm:aff id="Aff2">CIC-Centre de Pharmacologie Clinique et D’Evaluations Therapeutiques, AP-HM et Aix Marseille Université, Marseille, France</nlm:aff></affiliation></author><author><name sortKey="Ghorab, Karima" sort="Ghorab, Karima" uniqKey="Ghorab K" first="Karima" last="Ghorab">Karima Ghorab</name><affiliation><nlm:aff id="Aff3">CHU de Limoges - Hôpital Dupuytren, 2 Avenue Martin Luther King, 87042 Limoges, France</nlm:aff></affiliation></author><author><name sortKey="Al Moussawi, Mahmoud" sort="Al Moussawi, Mahmoud" uniqKey="Al Moussawi M" first="Mahmoud" last="Al-Moussawi">Mahmoud Al-Moussawi</name><affiliation><nlm:aff id="Aff4">CHU Lyon Sud, 165 Chemin du Grand Revoyet, 69495 Lyon, France</nlm:aff></affiliation></author><author><name sortKey="Tiffreau, Vincent" sort="Tiffreau, Vincent" uniqKey="Tiffreau V" first="Vincent" last="Tiffreau">Vincent Tiffreau</name><affiliation><nlm:aff id="Aff5">CHRU de Lille - Hôpital Roger Salengro, rue Emile Laine, 59037 Lille, France</nlm:aff></affiliation></author><author><name sortKey="Preudhomme, Marguerite" sort="Preudhomme, Marguerite" uniqKey="Preudhomme M" first="Marguerite" last="Preudhomme">Marguerite Preudhomme</name><affiliation><nlm:aff id="Aff5">CHRU de Lille - Hôpital Roger Salengro, rue Emile Laine, 59037 Lille, France</nlm:aff></affiliation></author><author><name sortKey="Magot, Armelle" sort="Magot, Armelle" uniqKey="Magot A" first="Armelle" last="Magot">Armelle Magot</name><affiliation><nlm:aff id="Aff6">CHU de Nantes - Hôtel Dieu, 1 place Alexis Ricordeau, 44093 Nantes, France</nlm:aff></affiliation></author><author><name sortKey="Leclair Visonneau, Laurene" sort="Leclair Visonneau, Laurene" uniqKey="Leclair Visonneau L" first="Laurène" last="Leclair-Visonneau">Laurène Leclair-Visonneau</name><affiliation><nlm:aff id="Aff5">CHRU de Lille - Hôpital Roger Salengro, rue Emile Laine, 59037 Lille, France</nlm:aff></affiliation></author><author><name sortKey="Stojkovic, Tanya" sort="Stojkovic, Tanya" uniqKey="Stojkovic T" first="Tanya" last="Stojkovic">Tanya Stojkovic</name><affiliation><nlm:aff id="Aff7">CHU de Paris - Groupe Hospitalier Pitié-Salpétrière, 47-83 boulevard de l’Hôpital, 75013 Paris, France</nlm:aff></affiliation></author><author><name sortKey="Bossi, Laura" sort="Bossi, Laura" uniqKey="Bossi L" first="Laura" last="Bossi">Laura Bossi</name><affiliation><nlm:aff id="Aff8">Admissions, 75017 Paris, France</nlm:aff></affiliation></author><author><name sortKey="Lehert, Philippe" sort="Lehert, Philippe" uniqKey="Lehert P" first="Philippe" last="Lehert">Philippe Lehert</name><affiliation><nlm:aff id="Aff9">Faculty of Medicine, The University of Melbourne, Grattan St, Melbourne, VIC 3010 Australia</nlm:aff></affiliation><affiliation><nlm:aff id="Aff10">Faculty of Economics, UCL Mons, Louvain, Belgium</nlm:aff></affiliation></author><author><name sortKey="Gilbert, Walter" sort="Gilbert, Walter" uniqKey="Gilbert W" first="Walter" last="Gilbert">Walter Gilbert</name><affiliation><nlm:aff id="Aff11">Carl M. Loeb University Professor Emeritus, Harvard University, Cambridge, MA 02138 USA</nlm:aff></affiliation></author><author><name sortKey="Bertrand, Viviane" sort="Bertrand, Viviane" uniqKey="Bertrand V" first="Viviane" last="Bertrand">Viviane Bertrand</name><affiliation><nlm:aff id="Aff12">Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris, France</nlm:aff></affiliation></author><author><name sortKey="Mandel, Jonas" sort="Mandel, Jonas" uniqKey="Mandel J" first="Jonas" last="Mandel">Jonas Mandel</name><affiliation><nlm:aff id="Aff12">Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris, France</nlm:aff></affiliation></author><author><name sortKey="Milet, Aude" sort="Milet, Aude" uniqKey="Milet A" first="Aude" last="Milet">Aude Milet</name><affiliation><nlm:aff id="Aff12">Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris, France</nlm:aff></affiliation></author><author><name sortKey="Hajj, Rodolphe" sort="Hajj, Rodolphe" uniqKey="Hajj R" first="Rodolphe" last="Hajj">Rodolphe Hajj</name><affiliation><nlm:aff id="Aff12">Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris, France</nlm:aff></affiliation></author><author><name sortKey="Boudiaf, Lamia" sort="Boudiaf, Lamia" uniqKey="Boudiaf L" first="Lamia" last="Boudiaf">Lamia Boudiaf</name><affiliation><nlm:aff id="Aff12">Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris, France</nlm:aff></affiliation></author><author><name sortKey="Scart Gres, Catherine" sort="Scart Gres, Catherine" uniqKey="Scart Gres C" first="Catherine" last="Scart-Grès">Catherine Scart-Grès</name><affiliation><nlm:aff id="Aff12">Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris, France</nlm:aff></affiliation></author><author><name sortKey="Nabirotchkin, Serguei" sort="Nabirotchkin, Serguei" uniqKey="Nabirotchkin S" first="Serguei" last="Nabirotchkin">Serguei Nabirotchkin</name><affiliation><nlm:aff id="Aff12">Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris, France</nlm:aff></affiliation></author><author><name sortKey="Guedj, Mickael" sort="Guedj, Mickael" uniqKey="Guedj M" first="Mickael" last="Guedj">Mickael Guedj</name><affiliation><nlm:aff id="Aff12">Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris, France</nlm:aff></affiliation></author><author><name sortKey="Chumakov, Ilya" sort="Chumakov, Ilya" uniqKey="Chumakov I" first="Ilya" last="Chumakov">Ilya Chumakov</name><affiliation><nlm:aff id="Aff12">Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris, France</nlm:aff></affiliation></author><author><name sortKey="Cohen, Daniel" sort="Cohen, Daniel" uniqKey="Cohen D" first="Daniel" last="Cohen">Daniel Cohen</name><affiliation><nlm:aff id="Aff12">Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris, France</nlm:aff></affiliation></author></titleStmt><publicationStmt><idno type="wicri:source">PMC</idno><idno type="pmid">27387831</idno><idno type="pmc">4937550</idno><idno type="url">http://www.ncbi.nlm.nih.gov/pmc/articles/PMC4937550</idno><idno type="RBID">PMC:4937550</idno><idno type="doi">10.1186/s13023-016-0463-6</idno><date when="2016">2016</date><idno type="wicri:Area/Pmc/Corpus">000964</idno><idno type="wicri:explorRef" wicri:stream="Pmc" wicri:step="Corpus" wicri:corpus="PMC">000964</idno></publicationStmt><sourceDesc><biblStruct><analytic><title xml:lang="en" level="a" type="main">Erratum to: An exploratory randomised double-blind and placebo-controlled phase 2 study of a combination of baclofen, naltrexone and sorbitol (PXT3003) in patients with Charcot-Marie-Tooth disease type 1A</title><author><name sortKey="Attarian, Shahram" sort="Attarian, Shahram" uniqKey="Attarian S" first="Shahram" last="Attarian">Shahram Attarian</name><affiliation><nlm:aff id="Aff1">Centre de référence des maladies neuromusculaires et de la SLA, Pôle des neurosciences Cliniques, AP-HM et Aix Marseille Université, Marseille, France</nlm:aff></affiliation></author><author><name sortKey="Vallat, Jean Michel" sort="Vallat, Jean Michel" uniqKey="Vallat J" first="Jean-Michel" last="Vallat">Jean-Michel Vallat</name><affiliation><nlm:aff id="Aff3">CHU de Limoges - Hôpital Dupuytren, 2 Avenue Martin Luther King, 87042 Limoges, France</nlm:aff></affiliation></author><author><name sortKey="Magy, Laurent" sort="Magy, Laurent" uniqKey="Magy L" first="Laurent" last="Magy">Laurent Magy</name><affiliation><nlm:aff id="Aff3">CHU de Limoges - Hôpital Dupuytren, 2 Avenue Martin Luther King, 87042 Limoges, France</nlm:aff></affiliation></author><author><name sortKey="Funalot, Benoit" sort="Funalot, Benoit" uniqKey="Funalot B" first="Benoît" last="Funalot">Benoît Funalot</name><affiliation><nlm:aff id="Aff3">CHU de Limoges - Hôpital Dupuytren, 2 Avenue Martin Luther King, 87042 Limoges, France</nlm:aff></affiliation></author><author><name sortKey="Gonnaud, Pierre Marie" sort="Gonnaud, Pierre Marie" uniqKey="Gonnaud P" first="Pierre-Marie" last="Gonnaud">Pierre-Marie Gonnaud</name><affiliation><nlm:aff id="Aff4">CHU Lyon Sud, 165 Chemin du Grand Revoyet, 69495 Lyon, France</nlm:aff></affiliation></author><author><name sortKey="Lacour, Arnaud" sort="Lacour, Arnaud" uniqKey="Lacour A" first="Arnaud" last="Lacour">Arnaud Lacour</name><affiliation><nlm:aff id="Aff5">CHRU de Lille - Hôpital Roger Salengro, rue Emile Laine, 59037 Lille, France</nlm:aff></affiliation></author><author><name sortKey="Pereon, Yann" sort="Pereon, Yann" uniqKey="Pereon Y" first="Yann" last="Péréon">Yann Péréon</name><affiliation><nlm:aff id="Aff6">CHU de Nantes - Hôtel Dieu, 1 place Alexis Ricordeau, 44093 Nantes, France</nlm:aff></affiliation></author><author><name sortKey="Dubourg, Odile" sort="Dubourg, Odile" uniqKey="Dubourg O" first="Odile" last="Dubourg">Odile Dubourg</name><affiliation><nlm:aff id="Aff7">CHU de Paris - Groupe Hospitalier Pitié-Salpétrière, 47-83 boulevard de l’Hôpital, 75013 Paris, France</nlm:aff></affiliation></author><author><name sortKey="Pouget, Jean" sort="Pouget, Jean" uniqKey="Pouget J" first="Jean" last="Pouget">Jean Pouget</name><affiliation><nlm:aff id="Aff1">Centre de référence des maladies neuromusculaires et de la SLA, Pôle des neurosciences Cliniques, AP-HM et Aix Marseille Université, Marseille, France</nlm:aff></affiliation></author><author><name sortKey="Micallef, Joelle" sort="Micallef, Joelle" uniqKey="Micallef J" first="Joëlle" last="Micallef">Joëlle Micallef</name><affiliation><nlm:aff id="Aff2">CIC-Centre de Pharmacologie Clinique et D’Evaluations Therapeutiques, AP-HM et Aix Marseille Université, Marseille, France</nlm:aff></affiliation></author><author><name sortKey="Franques, Jerome" sort="Franques, Jerome" uniqKey="Franques J" first="Jérôme" last="Franques">Jérôme Franques</name><affiliation><nlm:aff id="Aff1">Centre de référence des maladies neuromusculaires et de la SLA, Pôle des neurosciences Cliniques, AP-HM et Aix Marseille Université, Marseille, France</nlm:aff></affiliation></author><author><name sortKey="Lefebvre, Marie Noelle" sort="Lefebvre, Marie Noelle" uniqKey="Lefebvre M" first="Marie-Noëlle" last="Lefebvre">Marie-Noëlle Lefebvre</name><affiliation><nlm:aff id="Aff2">CIC-Centre de Pharmacologie Clinique et D’Evaluations Therapeutiques, AP-HM et Aix Marseille Université, Marseille, France</nlm:aff></affiliation></author><author><name sortKey="Ghorab, Karima" sort="Ghorab, Karima" uniqKey="Ghorab K" first="Karima" last="Ghorab">Karima Ghorab</name><affiliation><nlm:aff id="Aff3">CHU de Limoges - Hôpital Dupuytren, 2 Avenue Martin Luther King, 87042 Limoges, France</nlm:aff></affiliation></author><author><name sortKey="Al Moussawi, Mahmoud" sort="Al Moussawi, Mahmoud" uniqKey="Al Moussawi M" first="Mahmoud" last="Al-Moussawi">Mahmoud Al-Moussawi</name><affiliation><nlm:aff id="Aff4">CHU Lyon Sud, 165 Chemin du Grand Revoyet, 69495 Lyon, France</nlm:aff></affiliation></author><author><name sortKey="Tiffreau, Vincent" sort="Tiffreau, Vincent" uniqKey="Tiffreau V" first="Vincent" last="Tiffreau">Vincent Tiffreau</name><affiliation><nlm:aff id="Aff5">CHRU de Lille - Hôpital Roger Salengro, rue Emile Laine, 59037 Lille, France</nlm:aff></affiliation></author><author><name sortKey="Preudhomme, Marguerite" sort="Preudhomme, Marguerite" uniqKey="Preudhomme M" first="Marguerite" last="Preudhomme">Marguerite Preudhomme</name><affiliation><nlm:aff id="Aff5">CHRU de Lille - Hôpital Roger Salengro, rue Emile Laine, 59037 Lille, France</nlm:aff></affiliation></author><author><name sortKey="Magot, Armelle" sort="Magot, Armelle" uniqKey="Magot A" first="Armelle" last="Magot">Armelle Magot</name><affiliation><nlm:aff id="Aff6">CHU de Nantes - Hôtel Dieu, 1 place Alexis Ricordeau, 44093 Nantes, France</nlm:aff></affiliation></author><author><name sortKey="Leclair Visonneau, Laurene" sort="Leclair Visonneau, Laurene" uniqKey="Leclair Visonneau L" first="Laurène" last="Leclair-Visonneau">Laurène Leclair-Visonneau</name><affiliation><nlm:aff id="Aff5">CHRU de Lille - Hôpital Roger Salengro, rue Emile Laine, 59037 Lille, France</nlm:aff></affiliation></author><author><name sortKey="Stojkovic, Tanya" sort="Stojkovic, Tanya" uniqKey="Stojkovic T" first="Tanya" last="Stojkovic">Tanya Stojkovic</name><affiliation><nlm:aff id="Aff7">CHU de Paris - Groupe Hospitalier Pitié-Salpétrière, 47-83 boulevard de l’Hôpital, 75013 Paris, France</nlm:aff></affiliation></author><author><name sortKey="Bossi, Laura" sort="Bossi, Laura" uniqKey="Bossi L" first="Laura" last="Bossi">Laura Bossi</name><affiliation><nlm:aff id="Aff8">Admissions, 75017 Paris, France</nlm:aff></affiliation></author><author><name sortKey="Lehert, Philippe" sort="Lehert, Philippe" uniqKey="Lehert P" first="Philippe" last="Lehert">Philippe Lehert</name><affiliation><nlm:aff id="Aff9">Faculty of Medicine, The University of Melbourne, Grattan St, Melbourne, VIC 3010 Australia</nlm:aff></affiliation><affiliation><nlm:aff id="Aff10">Faculty of Economics, UCL Mons, Louvain, Belgium</nlm:aff></affiliation></author><author><name sortKey="Gilbert, Walter" sort="Gilbert, Walter" uniqKey="Gilbert W" first="Walter" last="Gilbert">Walter Gilbert</name><affiliation><nlm:aff id="Aff11">Carl M. Loeb University Professor Emeritus, Harvard University, Cambridge, MA 02138 USA</nlm:aff></affiliation></author><author><name sortKey="Bertrand, Viviane" sort="Bertrand, Viviane" uniqKey="Bertrand V" first="Viviane" last="Bertrand">Viviane Bertrand</name><affiliation><nlm:aff id="Aff12">Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris, France</nlm:aff></affiliation></author><author><name sortKey="Mandel, Jonas" sort="Mandel, Jonas" uniqKey="Mandel J" first="Jonas" last="Mandel">Jonas Mandel</name><affiliation><nlm:aff id="Aff12">Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris, France</nlm:aff></affiliation></author><author><name sortKey="Milet, Aude" sort="Milet, Aude" uniqKey="Milet A" first="Aude" last="Milet">Aude Milet</name><affiliation><nlm:aff id="Aff12">Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris, France</nlm:aff></affiliation></author><author><name sortKey="Hajj, Rodolphe" sort="Hajj, Rodolphe" uniqKey="Hajj R" first="Rodolphe" last="Hajj">Rodolphe Hajj</name><affiliation><nlm:aff id="Aff12">Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris, France</nlm:aff></affiliation></author><author><name sortKey="Boudiaf, Lamia" sort="Boudiaf, Lamia" uniqKey="Boudiaf L" first="Lamia" last="Boudiaf">Lamia Boudiaf</name><affiliation><nlm:aff id="Aff12">Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris, France</nlm:aff></affiliation></author><author><name sortKey="Scart Gres, Catherine" sort="Scart Gres, Catherine" uniqKey="Scart Gres C" first="Catherine" last="Scart-Grès">Catherine Scart-Grès</name><affiliation><nlm:aff id="Aff12">Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris, France</nlm:aff></affiliation></author><author><name sortKey="Nabirotchkin, Serguei" sort="Nabirotchkin, Serguei" uniqKey="Nabirotchkin S" first="Serguei" last="Nabirotchkin">Serguei Nabirotchkin</name><affiliation><nlm:aff id="Aff12">Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris, France</nlm:aff></affiliation></author><author><name sortKey="Guedj, Mickael" sort="Guedj, Mickael" uniqKey="Guedj M" first="Mickael" last="Guedj">Mickael Guedj</name><affiliation><nlm:aff id="Aff12">Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris, France</nlm:aff></affiliation></author><author><name sortKey="Chumakov, Ilya" sort="Chumakov, Ilya" uniqKey="Chumakov I" first="Ilya" last="Chumakov">Ilya Chumakov</name><affiliation><nlm:aff id="Aff12">Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris, France</nlm:aff></affiliation></author><author><name sortKey="Cohen, Daniel" sort="Cohen, Daniel" uniqKey="Cohen D" first="Daniel" last="Cohen">Daniel Cohen</name><affiliation><nlm:aff id="Aff12">Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris, France</nlm:aff></affiliation></author></analytic><series><title level="j">Orphanet Journal of Rare Diseases</title><idno type="eISSN">1750-1172</idno><imprint><date when="2016">2016</date></imprint></series></biblStruct></sourceDesc></fileDesc><profileDesc><textClass></textClass></profileDesc></teiHeader><back><div1 type="bibliography"><listBibl><biblStruct><analytic><author><name sortKey="Attarian, S" uniqKey="Attarian S">S Attarian</name></author><author><name sortKey="Vallat, Jm" uniqKey="Vallat J">JM Vallat</name></author><author><name sortKey="Magy, L" uniqKey="Magy L">L Magy</name></author><author><name sortKey="Funalot, B" uniqKey="Funalot B">B Funalot</name></author><author><name sortKey="Gonnaud, Pm" uniqKey="Gonnaud P">PM Gonnaud</name></author><author><name sortKey="Lacour, A" uniqKey="Lacour A">A Lacour</name></author><author><name sortKey="Pereon, Y" uniqKey="Pereon Y">Y Péréon</name></author><author><name sortKey="Dubourg, O" uniqKey="Dubourg O">O Dubourg</name></author><author><name sortKey="Pouget, J" uniqKey="Pouget J">J Pouget</name></author><author><name sortKey="Micallef, J" uniqKey="Micallef J">J Micallef</name></author><author><name sortKey="Franques, J" uniqKey="Franques J">J Franques</name></author><author><name sortKey="Lefebvre, Mn" uniqKey="Lefebvre M">MN Lefebvre</name></author><author><name sortKey="Ghorab, K" uniqKey="Ghorab K">K Ghorab</name></author><author><name sortKey="Al Moussawi, M" uniqKey="Al Moussawi M">M Al-Moussawi</name></author><author><name sortKey="Tiffreau, V" uniqKey="Tiffreau V">V Tiffreau</name></author><author><name sortKey="Preudhomme, M" uniqKey="Preudhomme M">M Preudhomme</name></author><author><name sortKey="Magot, A" uniqKey="Magot A">A Magot</name></author><author><name sortKey="Leclair Visonneau, L" uniqKey="Leclair Visonneau L">L Leclair-Visonneau</name></author><author><name sortKey="Stojkovic, T" uniqKey="Stojkovic T">T Stojkovic</name></author><author><name sortKey="Bossi, L" uniqKey="Bossi L">L Bossi</name></author><author><name sortKey="Lehert, P" uniqKey="Lehert P">P Lehert</name></author><author><name sortKey="Gilbert, W" uniqKey="Gilbert W">W Gilbert</name></author><author><name sortKey="Bertrand, V" uniqKey="Bertrand V">V Bertrand</name></author><author><name sortKey="Mandel, J" uniqKey="Mandel J">J Mandel</name></author><author><name sortKey="Milet, A" uniqKey="Milet A">A Milet</name></author><author><name sortKey="Hajj, R" uniqKey="Hajj R">R Hajj</name></author><author><name sortKey="Boudiaf, L" uniqKey="Boudiaf L">L Boudiaf</name></author><author><name sortKey="Scart Gres, C" uniqKey="Scart Gres C">C Scart-Grès</name></author><author><name sortKey="Nabirotchkin, S" uniqKey="Nabirotchkin S">S Nabirotchkin</name></author><author><name sortKey="Guedj, M" uniqKey="Guedj M">M Guedj</name></author><author><name sortKey="Chumakov, I" uniqKey="Chumakov I">I Chumakov</name></author><author><name sortKey="Cohen, D" uniqKey="Cohen D">D Cohen</name></author></analytic></biblStruct></listBibl></div1></back></TEI><pmc article-type="correction"><pmc-dir>properties open_access</pmc-dir>
<front><journal-meta><journal-id journal-id-type="nlm-ta">Orphanet J Rare Dis</journal-id><journal-id journal-id-type="iso-abbrev">Orphanet J Rare Dis</journal-id><journal-title-group><journal-title>Orphanet Journal of Rare Diseases</journal-title></journal-title-group><issn pub-type="epub">1750-1172</issn><publisher><publisher-name>BioMed Central</publisher-name><publisher-loc>London</publisher-loc></publisher></journal-meta><article-meta><article-id pub-id-type="pmid">27387831</article-id><article-id pub-id-type="pmc">4937550</article-id><article-id pub-id-type="publisher-id">463</article-id><article-id pub-id-type="doi">10.1186/s13023-016-0463-6</article-id><article-categories><subj-group subj-group-type="heading"><subject>Erratum</subject></subj-group></article-categories><title-group><article-title>Erratum to: An exploratory randomised double-blind and placebo-controlled phase 2 study of a combination of baclofen, naltrexone and sorbitol (PXT3003) in patients with Charcot-Marie-Tooth disease type 1A</article-title></title-group><contrib-group><contrib contrib-type="author" equal-contrib="yes"><name><surname>Attarian</surname><given-names>Shahram</given-names></name><xref ref-type="aff" rid="Aff1"></xref></contrib><contrib contrib-type="author"><name><surname>Vallat</surname><given-names>Jean-Michel</given-names></name><xref ref-type="aff" rid="Aff3"></xref></contrib><contrib contrib-type="author"><name><surname>Magy</surname><given-names>Laurent</given-names></name><xref ref-type="aff" rid="Aff3"></xref></contrib><contrib contrib-type="author"><name><surname>Funalot</surname><given-names>Benoît</given-names></name><xref ref-type="aff" rid="Aff3"></xref></contrib><contrib contrib-type="author"><name><surname>Gonnaud</surname><given-names>Pierre-Marie</given-names></name><xref ref-type="aff" rid="Aff4"></xref></contrib><contrib contrib-type="author"><name><surname>Lacour</surname><given-names>Arnaud</given-names></name><xref ref-type="aff" rid="Aff5"></xref></contrib><contrib contrib-type="author"><name><surname>Péréon</surname><given-names>Yann</given-names></name><xref ref-type="aff" rid="Aff6"></xref></contrib><contrib contrib-type="author"><name><surname>Dubourg</surname><given-names>Odile</given-names></name><xref ref-type="aff" rid="Aff7"></xref></contrib><contrib contrib-type="author"><name><surname>Pouget</surname><given-names>Jean</given-names></name><xref ref-type="aff" rid="Aff1"></xref></contrib><contrib contrib-type="author"><name><surname>Micallef</surname><given-names>Joëlle</given-names></name><xref ref-type="aff" rid="Aff2"></xref></contrib><contrib contrib-type="author"><name><surname>Franques</surname><given-names>Jérôme</given-names></name><xref ref-type="aff" rid="Aff1"></xref></contrib><contrib contrib-type="author"><name><surname>Lefebvre</surname><given-names>Marie-Noëlle</given-names></name><xref ref-type="aff" rid="Aff2"></xref></contrib><contrib contrib-type="author"><name><surname>Ghorab</surname><given-names>Karima</given-names></name><xref ref-type="aff" rid="Aff3"></xref></contrib><contrib contrib-type="author"><name><surname>Al-Moussawi</surname><given-names>Mahmoud</given-names></name><xref ref-type="aff" rid="Aff4"></xref></contrib><contrib contrib-type="author"><name><surname>Tiffreau</surname><given-names>Vincent</given-names></name><xref ref-type="aff" rid="Aff5"></xref></contrib><contrib contrib-type="author"><name><surname>Preudhomme</surname><given-names>Marguerite</given-names></name><xref ref-type="aff" rid="Aff5"></xref></contrib><contrib contrib-type="author"><name><surname>Magot</surname><given-names>Armelle</given-names></name><xref ref-type="aff" rid="Aff6"></xref></contrib><contrib contrib-type="author"><name><surname>Leclair-Visonneau</surname><given-names>Laurène</given-names></name><xref ref-type="aff" rid="Aff5"></xref></contrib><contrib contrib-type="author"><name><surname>Stojkovic</surname><given-names>Tanya</given-names></name><xref ref-type="aff" rid="Aff7"></xref></contrib><contrib contrib-type="author"><name><surname>Bossi</surname><given-names>Laura</given-names></name><xref ref-type="aff" rid="Aff8"></xref></contrib><contrib contrib-type="author"><name><surname>Lehert</surname><given-names>Philippe</given-names></name><xref ref-type="aff" rid="Aff9"></xref><xref ref-type="aff" rid="Aff10"></xref></contrib><contrib contrib-type="author"><name><surname>Gilbert</surname><given-names>Walter</given-names></name><xref ref-type="aff" rid="Aff11"></xref></contrib><contrib contrib-type="author" equal-contrib="yes"><name><surname>Bertrand</surname><given-names>Viviane</given-names></name><xref ref-type="aff" rid="Aff12"></xref></contrib><contrib contrib-type="author"><name><surname>Mandel</surname><given-names>Jonas</given-names></name><xref ref-type="aff" rid="Aff12"></xref></contrib><contrib contrib-type="author"><name><surname>Milet</surname><given-names>Aude</given-names></name><xref ref-type="aff" rid="Aff12"></xref></contrib><contrib contrib-type="author"><name><surname>Hajj</surname><given-names>Rodolphe</given-names></name><xref ref-type="aff" rid="Aff12"></xref></contrib><contrib contrib-type="author"><name><surname>Boudiaf</surname><given-names>Lamia</given-names></name><xref ref-type="aff" rid="Aff12"></xref></contrib><contrib contrib-type="author"><name><surname>Scart-Grès</surname><given-names>Catherine</given-names></name><xref ref-type="aff" rid="Aff12"></xref></contrib><contrib contrib-type="author"><name><surname>Nabirotchkin</surname><given-names>Serguei</given-names></name><xref ref-type="aff" rid="Aff12"></xref></contrib><contrib contrib-type="author" equal-contrib="yes"><name><surname>Guedj</surname><given-names>Mickael</given-names></name><xref ref-type="aff" rid="Aff12"></xref></contrib><contrib contrib-type="author"><name><surname>Chumakov</surname><given-names>Ilya</given-names></name><xref ref-type="aff" rid="Aff12"></xref></contrib><contrib contrib-type="author" corresp="yes"><name><surname>Cohen</surname><given-names>Daniel</given-names></name><address><email>daniel.cohen@pharnext.com</email></address><xref ref-type="aff" rid="Aff12"></xref></contrib><aff id="Aff1"><label></label>Centre de référence des maladies neuromusculaires et de la SLA, Pôle des neurosciences Cliniques, AP-HM et Aix Marseille Université, Marseille, France</aff><aff id="Aff2"><label></label>CIC-Centre de Pharmacologie Clinique et D’Evaluations Therapeutiques, AP-HM et Aix Marseille Université, Marseille, France</aff><aff id="Aff3"><label></label>CHU de Limoges - Hôpital Dupuytren, 2 Avenue Martin Luther King, 87042 Limoges, France</aff><aff id="Aff4"><label></label>CHU Lyon Sud, 165 Chemin du Grand Revoyet, 69495 Lyon, France</aff><aff id="Aff5"><label></label>CHRU de Lille - Hôpital Roger Salengro, rue Emile Laine, 59037 Lille, France</aff><aff id="Aff6"><label></label>CHU de Nantes - Hôtel Dieu, 1 place Alexis Ricordeau, 44093 Nantes, France</aff><aff id="Aff7"><label></label>CHU de Paris - Groupe Hospitalier Pitié-Salpétrière, 47-83 boulevard de l’Hôpital, 75013 Paris, France</aff><aff id="Aff8"><label></label>Admissions, 75017 Paris, France</aff><aff id="Aff9"><label></label>Faculty of Medicine, The University of Melbourne, Grattan St, Melbourne, VIC 3010 Australia</aff><aff id="Aff10"><label></label>Faculty of Economics, UCL Mons, Louvain, Belgium</aff><aff id="Aff11"><label></label>Carl M. Loeb University Professor Emeritus, Harvard University, Cambridge, MA 02138 USA</aff><aff id="Aff12"><label></label>Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris, France</aff></contrib-group><pub-date pub-type="epub"><day>7</day><month>7</month><year>2016</year></pub-date><pub-date pub-type="pmc-release"><day>7</day><month>7</month><year>2016</year></pub-date><pub-date pub-type="collection"><year>2016</year></pub-date><volume>11</volume><elocation-id>92</elocation-id><history><date date-type="received"><day>16</day><month>5</month><year>2016</year></date><date date-type="accepted"><day>16</day><month>5</month><year>2016</year></date></history><permissions><copyright-statement>© The Author(s). 2016</copyright-statement><license license-type="OpenAccess"><license-p><bold>Open Access</bold>This article is distributed under the terms of the Creative Commons Attribution 4.0 International License (<ext-link ext-link-type="uri" xlink:href="http://creativecommons.org/licenses/by/4.0/">http://creativecommons.org/licenses/by/4.0/</ext-link>), which permits unrestricted use, distribution, and reproduction in any medium, provided you give appropriate credit to the original author(s) and the source, provide a link to the Creative Commons license, and indicate if changes were made. The Creative Commons Public Domain Dedication waiver (<ext-link ext-link-type="uri" xlink:href="http://creativecommons.org/publicdomain/zero/1.0/">http://creativecommons.org/publicdomain/zero/1.0/</ext-link>) applies to the data made available in this article, unless otherwise stated.</license-p></license></permissions><related-article related-article-type="corrected-article" id="d30e69" ext-link-type="doi" xlink:href="10.1186/s13023-014-0199-0"></related-article><custom-meta-group><custom-meta><meta-name>issue-copyright-statement</meta-name><meta-value>© The Author(s) 2016</meta-value></custom-meta></custom-meta-group></article-meta></front><body><p>Unfortunately, the original version of this article [<xref ref-type="bibr" rid="CR1">1</xref>] contained an error due to a typographical error in the computer code used. This meant the percentage improvement over baseline of the endpoints CMTNS, ONLS, 9HPT and DML was slightly increased. Therefore some of the values in Tables <xref rid="Tab1" ref-type="table">3</xref>, <xref rid="Tab2" ref-type="table">4</xref>, Additional file <xref rid="MOESM1" ref-type="media">4</xref>: Table S4 and Fig. <xref rid="Fig1" ref-type="fig">4</xref> are incorrect.<table-wrap id="Tab1"><label>Table 3</label><caption><p>Response to PXT3003 on efficacy outcomes in treatment groups, with comparisons of active doses versus Placebo (Full Analysis Set, <italic>n</italic> = 80)</p></caption><table frame="hsides" rules="groups"><thead><tr><th></th><th colspan="4">Mean % of improvement</th><th colspan="2">PXT3003 LD versus Placebo</th><th colspan="2">PXT3003 ID versus Placebo</th><th colspan="2">PXT3003 HD versus Placebo</th><th colspan="2">Dose-effect</th></tr><tr><th rowspan="2"></th><th>Placebo</th><th>PXT3003 LD</th><th>PXT3003 ID</th><th>PXT3003 HD</th><th rowspan="2">Estimate</th><th rowspan="2"><italic>P</italic>-value</th><th rowspan="2">Estimate</th><th rowspan="2"><italic>P</italic>-value</th><th rowspan="2">Estimate</th><th rowspan="2"><italic>P</italic>-value</th><th rowspan="2">Correlation</th><th rowspan="2"><italic>P</italic>-value</th></tr><tr><th>(<italic>n</italic> = 19)</th><th>(<italic>n</italic> = 21)</th><th>(<italic>n</italic> = 21)</th><th>(<italic>n</italic> = 19)</th></tr></thead><tbody><tr><td>CMTNS</td><td>−0.25 (17.3)</td><td>−3.8 (20.4)</td><td>−5.8 (17.7)</td><td><bold>5.2 (12.5)</bold></td><td>−2.6 (−11.9;7.6)</td><td>0.67</td><td>−3.1 (−11.0;5.4)</td><td>0.74</td><td>5.5 (−3.4;15.2)</td><td>0.16</td><td>0.54</td><td>0.30</td></tr><tr><td>ONLS</td><td>−11.8 (33.7)</td><td>−12.7 (31.7)</td><td>1.2 (16.7)</td><td><bold>6.8 (18.2)</bold></td><td>−3.9 (−14.2;7.6)</td><td>0.72</td><td>6.9 (−3.8;18.8)</td><td>0.15</td><td>14.4 (0.55;30.2)</td><td>0.043*</td><td>0.28</td><td>0.006*</td></tr><tr><td>6MWT (m)</td><td>9.0 (8.3)</td><td>6.2 (8.3)</td><td>6.4 (9.4)</td><td><bold>9.9 (6.9)</bold></td><td>−2.4 (−6.2;1.5)</td><td>0.85</td><td>−2.4 (−6.6;2.0)</td><td>0.82</td><td>0.7 (−3.2;4.7)</td><td>0.38</td><td>0.11</td><td>0.16</td></tr><tr><td>9HPT (s)</td><td>3.6 (10.9)</td><td>−2.5 (12)</td><td>4.4 (9.5)</td><td><bold>6.1 (10.6)</bold></td><td>−4.6 (−10.3;1.5)</td><td>0.89</td><td>−0.2 (−5.3;5.2)</td><td>0.52</td><td>0.3 (−5.7;6.6)</td><td>0.47</td><td>0.15</td><td>0.092</td></tr><tr><td>Ankle Dorsiflexion (Nm)</td><td>20.2 (88.4)</td><td>−3.6 (43.0)</td><td><bold>81.5 (369.6)</bold></td><td>20.4 (64.1)</td><td>−4.0 (−21.7;17.8)</td><td>0.63</td><td>11.4 (−15.4;46.8)</td><td>0.26</td><td>8.2 (−13.8;35.9)</td><td>0.28</td><td>0.11</td><td>0.16</td></tr><tr><td>Grip (kg)</td><td>9.9 (24.2)</td><td>1.3 (15.6)</td><td>4.7 (12.5)</td><td><bold>11.7 (18.1)</bold></td><td>−7.1 (−15.6;2.1)</td><td>0.90</td><td>−3.6 (−11.8;5.4)</td><td>0.75</td><td>1.6 (−7.7;11.9)</td><td>0.39</td><td>0.12</td><td>0.15</td></tr><tr><td>CMAP (milliV)</td><td>34.4 (62.0)</td><td>1.4 (38.7)</td><td>22.9 (62.6)</td><td><bold>64.2 (208.5)</bold></td><td>−25.1 (−44.8;1.5)</td><td>0.94</td><td>−9.2 (−27.3;13.5)</td><td>0.77</td><td>−5.1 (−27.1;23.6)</td><td>0.63</td><td>−0.001</td><td>0.50</td></tr><tr><td>MCV (m/s)</td><td>3.7 (8.5)</td><td>3.0 (11.5)</td><td>5.7 (12.3)</td><td><bold>9.0 (17.6)</bold></td><td>−1.0 (−6.5;4.9)</td><td>0.61</td><td>0.5 (−4.8;6.2)</td><td>0.44</td><td>2.8 (−3.4;9.4)</td><td>0.23</td><td>0.11</td><td>0.18</td></tr><tr><td>DML (ms)</td><td>−0.33 (8.7)</td><td>0.33 (16.1)</td><td><bold>8.3 (18.1)</bold></td><td>5 (15.2)</td><td>3.4 (−4.3;11.7)</td><td>0.24</td><td>13.8 (4.2;24.3)</td><td>0.009*</td><td>8.0 (0.59;16.0)</td><td>0.038*</td><td>0.21</td><td>0.035*</td></tr><tr><td>SNAP (microV)</td><td>12.4 (121.7)</td><td>11.5 (88.2)</td><td><bold>23.3 (128.4)</bold></td><td>5.2 (69.0)</td><td>−1.2 (−42.9;71.0)</td><td>0.52</td><td>8.7 (−31.2;71.6)</td><td>0.38</td><td>13.9 (−24.1;71.0)</td><td>0.29</td><td>0.09</td><td>0.30</td></tr><tr><td>SCV (m/s)</td><td>3.4 (11.0)</td><td>5.3 (11.2)</td><td>29.5 (63.4)</td><td><bold>30.5 (10.0)</bold></td><td>1.5 (−5.8;9.4)</td><td>0.36</td><td>17.5 (−5.5;46.2)</td><td>0.11†</td><td>26.6 (15.5;38.8)</td><td>0.00037*</td><td>0.42</td><td>0.01*</td></tr></tbody></table><table-wrap-foot><p>Data are mean % (s.d.) of improvement for each treatment group. Differences between treatment groups were assessed by Analysis of Covariance (ANCOVA) on log-transformed values by adjusting for baseline values. Estimates were provided as mean percentage change over baseline (90 % CI). Dose-effect was tested through Spearman’s rank correlation. <italic>P</italic>-values are one-tailed. *<italic>P</italic> < 0.05; Shading = best improvement within dosages. <italic>CMTNS</italic> Charcot-Marie-Tooth Neuropathy Score, <italic>ONLS</italic> Overall Neuropathy Limitations Scale, <italic>6MWT</italic> 6-Minute Walk Test, <italic>9HPT</italic> 9-Hole Peg Test, <italic>CMAP</italic> Amplitudes of Compound Muscle Action Potentials, <italic>MCV</italic> Motor Conduction Velocity, <italic>DML</italic> Distal Motor Latency, <italic>SNAP</italic> Amplitudes of Sensory Nerve Action Potentials, <italic>SCV</italic> Sensitive Conduction Velocity</p></table-wrap-foot></table-wrap><table-wrap id="Tab2"><label>Table 4</label><caption><p>Response to PXT3003 on efficacy outcomes in HD and in PLI, with comparisons of HD versus PLI (Full Analysis Set, <italic>n</italic> = 80)</p></caption><table frame="hsides" rules="groups"><thead><tr><th></th><th colspan="2">Mean % of improvement</th><th colspan="2">PXT3003 HD versus PLI</th></tr><tr><th rowspan="2"></th><th>PLI</th><th>PXT3003 HD</th><th rowspan="2">Estimate</th><th rowspan="2"><italic>P</italic>-value</th></tr><tr><th>(<italic>n</italic> = 61)</th><th>(<italic>n</italic> = 19)</th></tr></thead><tbody><tr><td>CMTNS</td><td>−3.4 (18.4)</td><td><bold>5.2 (12.5)</bold></td><td>8.0 (0.4;16.2)</td><td>0.042*</td></tr><tr><td>ONLS</td><td>−7.7 (28.5)</td><td><bold>6.8 (18.2)</bold></td><td>12.1 (2.0;23.2)</td><td>0.024*</td></tr><tr><td>6MWT (m)</td><td>7.1 (8.6)</td><td><bold>9.9 (6.9)</bold></td><td>2.6 (−0.73;6.1)</td><td>0.099</td></tr><tr><td>9HPT (s)</td><td>1.8 (11.1)</td><td><bold>6.1 (10.6)</bold></td><td>1.2 (−3.4;6.0)</td><td>0.33</td></tr><tr><td>Ankle Dorsiflexion (Nm)</td><td><bold>33.1 (223.2)</bold></td><td>20.4 (64.1)</td><td>5.5 (−12.8;27.7)</td><td>0.32</td></tr><tr><td>Grip (kg)</td><td>5.1 (17.9)</td><td><bold>11.7 (18.1)</bold></td><td>6.0 (−1.2;13.7)</td><td>0.088</td></tr><tr><td>CMAP (milliV)</td><td>19.6 (56.5)</td><td><bold>64.2 (208.5)</bold></td><td>6.6 (−15.8;35.1)</td><td>0.33</td></tr><tr><td>MCV (m/s)</td><td>4.2 (10.9)</td><td><bold>9.0 (17.6)</bold></td><td>2.5 (−2.4;7.7)</td><td>0.21</td></tr><tr><td>DML (ms)</td><td>3 (15.3)</td><td><bold>5 (15.2)</bold></td><td>2.2 (−5.1;10.0)</td><td>0.31</td></tr><tr><td>SNAP (microV)</td><td><bold>15.9 (110.2)</bold></td><td>5.2 (69.0)</td><td>12.0 (−23.9;64.9)</td><td>0.31</td></tr><tr><td>SCV (m/s)</td><td>12.7 (38.0)</td><td><bold>30.5 (10.0)</bold></td><td>20.1 (2.4;40.8)</td><td>0.030*</td></tr></tbody></table><table-wrap-foot><p>Data are mean % (s.d.) of improvement for HD and for PLI after 12 months. Differences between treatment groups were assessed by Analysis of Covariance (ANCOVA) on log-transformed values by adjusting for baseline values. Estimates were provided as mean percentage change over baseline (90 % CI). <italic>P</italic>-values are one-tailed. *<italic>P</italic> < 0.05; Shading = best improvement within groups. <italic>CMTNS</italic> Charcot-Marie-Tooth Neuropathy Score, <italic>ONLS</italic> Overall Neuropathy Limitations Scale, <italic>6MWT</italic> 6-Minute Walk Test, <italic>9HPT</italic> 9-Hole Peg Test, <italic>CMAP</italic> Amplitudes of Compound Muscle Action Potentials, <italic>MCV</italic> Motor Conduction Velocity, <italic>DML</italic> Distal Motor Latency, <italic>SNAP</italic> Amplitudes of Sensory Nerve Action Potentials, <italic>SCV</italic> Sensitive Conduction Velocity</p></table-wrap-foot></table-wrap><fig id="Fig1"><label>Fig. 4</label><caption><p>Response to PXT3003 on clinical scales (Full Analysis Set, <italic>n</italic> = 80). Mean % (s.e.m.) of improvement from baseline per group at 12 months for CMTNS (<bold>a</bold>) and ONLS (<bold>b</bold>). Sample sizes: Placebo (<italic>n</italic> = 19), LD (<italic>n</italic> = 21), ID (<italic>n</italic> = 21), HD (<italic>n</italic> = 19)</p></caption><graphic xlink:href="13023_2016_463_Fig1_HTML" id="MO3"></graphic></fig></p><p>However this error has no bearing on statistical outcome of the study, the conclusions or text of the manuscript. Correct versions of Tables <xref rid="Tab1" ref-type="table">3</xref>, <xref rid="Tab2" ref-type="table">4</xref> and Fig. <xref rid="Fig1" ref-type="fig">4</xref> can be seen below and Additional file <xref rid="MOESM1" ref-type="media">4</xref> accessed using the link below.</p></body><back><app-group><app id="App1"><sec id="Sec1"><title>Additional file</title><p><media position="anchor" xlink:href="13023_2016_463_MOESM1_ESM.doc" id="MOESM1"><label>Additional file 4: Table S4.</label><caption><p>Response to PXT3003 on efficacy outcomes (Full Analysis Set, <italic>n</italic> = 80). Data are mean (s.d.) baseline and final values, and % (s.d.) of improvement for each treatment group and PLI. Differences between treatment groups were assessed by Analysis of Covariance (Ancova) on log-transformed values by adjusting for baseline values. Estimates were provided as mean percentage change over baseline (90 % CI). Dose-effect was tested through Spearman’s rank correlation. <italic>P</italic>-values are one-tailed. CMTNS = Charcot-Marie-Tooth Neuropathy Score; ONLS = Overall Neuropathy Limitations Scale; 6MWT = 6-Minute Walk Test; 9HPT = 9-Hole Peg Test; CMAP = Amplitudes of Compound Muscle Action Potentials; MCV = Motor Conduction Velocity; DML = Distal Motor Latency; SNAP = Amplitudes of Sensory Nerve Action Potentials; SCV = Sensitive Conduction Velocity; VAS = Visual Analog Scale; CGI = Clinical Global Impression. (DOC 168 kb)</p></caption></media></p></sec></app></app-group><fn-group><fn><p>The online version of the original article can be found under doi:10.1186/s13023-014-0199-0.</p></fn></fn-group><ref-list id="Bib1"><title>References</title><ref id="CR1"><label>1.</label><element-citation publication-type="journal"><person-group person-group-type="author"><name><surname>Attarian</surname><given-names>S</given-names></name><name><surname>Vallat</surname><given-names>JM</given-names></name><name><surname>Magy</surname><given-names>L</given-names></name><name><surname>Funalot</surname><given-names>B</given-names></name><name><surname>Gonnaud</surname><given-names>PM</given-names></name><name><surname>Lacour</surname><given-names>A</given-names></name><name><surname>Péréon</surname><given-names>Y</given-names></name><name><surname>Dubourg</surname><given-names>O</given-names></name><name><surname>Pouget</surname><given-names>J</given-names></name><name><surname>Micallef</surname><given-names>J</given-names></name><name><surname>Franques</surname><given-names>J</given-names></name><name><surname>Lefebvre</surname><given-names>MN</given-names></name><name><surname>Ghorab</surname><given-names>K</given-names></name><name><surname>Al-Moussawi</surname><given-names>M</given-names></name><name><surname>Tiffreau</surname><given-names>V</given-names></name><name><surname>Preudhomme</surname><given-names>M</given-names></name><name><surname>Magot</surname><given-names>A</given-names></name><name><surname>Leclair-Visonneau</surname><given-names>L</given-names></name><name><surname>Stojkovic</surname><given-names>T</given-names></name><name><surname>Bossi</surname><given-names>L</given-names></name><name><surname>Lehert</surname><given-names>P</given-names></name><name><surname>Gilbert</surname><given-names>W</given-names></name><name><surname>Bertrand</surname><given-names>V</given-names></name><name><surname>Mandel</surname><given-names>J</given-names></name><name><surname>Milet</surname><given-names>A</given-names></name><name><surname>Hajj</surname><given-names>R</given-names></name><name><surname>Boudiaf</surname><given-names>L</given-names></name><name><surname>Scart-Grès</surname><given-names>C</given-names></name><name><surname>Nabirotchkin</surname><given-names>S</given-names></name><name><surname>Guedj</surname><given-names>M</given-names></name><name><surname>Chumakov</surname><given-names>I</given-names></name><name><surname>Cohen</surname><given-names>D</given-names></name></person-group><article-title>An exploratory randomised double-blind and placebo-controlled phase 2 study of a combination of baclofen, naltrexone and sorbitol (PXT3003) in patients with Charcot-Marie-Tooth disease type 1A</article-title><source>Orphanet J Rare Dis.</source><year>2014</year><volume>9</volume><fpage>199</fpage><pub-id pub-id-type="doi">10.1186/s13023-014-0199-0</pub-id><pub-id pub-id-type="pmid">25519680</pub-id></element-citation></ref></ref-list></back></pmc></record>Pour manipuler ce document sous Unix (Dilib)
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