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Development of multinational definitions of minimal clinically important improvement and patient acceptable symptomatic state in osteoarthritis.

Identifieur interne : 002D24 ( PubMed/Checkpoint ); précédent : 002D23; suivant : 002D25

Development of multinational definitions of minimal clinically important improvement and patient acceptable symptomatic state in osteoarthritis.

Auteurs : Nicholas Bellamy [Australie] ; Marc Hochberg [États-Unis] ; Florence Tubach [France] ; Emilio Martin-Mola [Espagne] ; Hassane Awada [Liban] ; Claire Bombardier [Canada] ; Najia Hajjaj-Hassouni [Maroc] ; Isabelle Logeart [France] ; Marco Matucci-Cerinic [Italie] ; Mart Van De Laar [Pays-Bas] ; Désirée Van Der Heijde [Pays-Bas] ; Maxime Dougados [France]

Source :

RBID : pubmed:25581339

Descripteurs français

English descriptors

Abstract

The ability to interpret scores from patient-reported outcome measures at the individual patient level depends on the availability of valid, clinically meaningful benchmarks of response and state attainment. The goal was to develop multinational estimates for minimal clinically important improvement (MCII) and patient acceptable symptomatic state (PASS).

DOI: 10.1002/acr.22538
PubMed: 25581339


Affiliations:


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pubmed:25581339

Le document en format XML

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<Abstract>
<AbstractText Label="OBJECTIVE" NlmCategory="OBJECTIVE">The ability to interpret scores from patient-reported outcome measures at the individual patient level depends on the availability of valid, clinically meaningful benchmarks of response and state attainment. The goal was to develop multinational estimates for minimal clinically important improvement (MCII) and patient acceptable symptomatic state (PASS).</AbstractText>
<AbstractText Label="METHODS" NlmCategory="METHODS">A multinational sample of patients with osteoarthritis (OA) was evaluated before and 4 weeks after treatment with nonsteroidal antiinflammatory drugs. Patients completed either the Western Ontario and McMaster Osteoarthritis Index (WOMAC) numerical rating scale 3.1 (hip and knee OA) or the Australian/Canadian Index (AUSCAN) numerical rating scale 3.1 (hand OA) before and after treatment. Patients rated the clinical importance of their response to treatment and their satisfaction with the health state achieved, from which multinational MCII and PASS estimates were calculated for both the WOMAC and AUSCAN indices.</AbstractText>
<AbstractText Label="RESULTS" NlmCategory="RESULTS">A total of 609 patients from 7 countries participated in the study. MCII and PASS estimates varied slightly by instrument and subscale. Absolute (percentage) change for MCII ranged 6-9 (10% to 17%) for WOMAC and 4-9 (8% to 15%) for AUSCAN. PASS estimates ranged 39-48 for WOMAC and 38-45 for AUSCAN. Some between-country variation was observed in MCII and PASS.</AbstractText>
<AbstractText Label="CONCLUSION" NlmCategory="CONCLUSIONS">Preliminary multinational estimates for MCII and PASS have been developed for several countries. Further research is required to evaluate the robustness, temporal consistency, and age- and sex-dependency of the preliminary estimates as well as their generalizability to other countries, languages, cultures, regions, and other condition-specific outcome measures.</AbstractText>
<CopyrightInformation>© 2015, American College of Rheumatology.</CopyrightInformation>
</Abstract>
<AuthorList CompleteYN="Y">
<Author ValidYN="Y">
<LastName>Bellamy</LastName>
<ForeName>Nicholas</ForeName>
<Initials>N</Initials>
<AffiliationInfo>
<Affiliation>University of Queensland School of Medicine, Brisbane, Queensland, Australia, and Royal Brisbane and Women's Hospital, Herston, Queensland, Australia.</Affiliation>
</AffiliationInfo>
</Author>
<Author ValidYN="Y">
<LastName>Hochberg</LastName>
<ForeName>Marc</ForeName>
<Initials>M</Initials>
<AffiliationInfo>
<Affiliation>University of Maryland School of Medicine, Baltimore.</Affiliation>
</AffiliationInfo>
</Author>
<Author ValidYN="Y">
<LastName>Tubach</LastName>
<ForeName>Florence</ForeName>
<Initials>F</Initials>
<AffiliationInfo>
<Affiliation>Université Paris Diderot, Sorbonne Paris Cité, INSERM, UMR-S 1123, INSERM, CIC 1425-EC, UMR-S 1123, and AP-HP Hôpital Bichat, Paris, France.</Affiliation>
</AffiliationInfo>
</Author>
<Author ValidYN="Y">
<LastName>Martin-Mola</LastName>
<ForeName>Emilio</ForeName>
<Initials>E</Initials>
<AffiliationInfo>
<Affiliation>Hospital Universitario La Paz and Universidad Autónoma Madrid, Madrid, Spain.</Affiliation>
</AffiliationInfo>
</Author>
<Author ValidYN="Y">
<LastName>Awada</LastName>
<ForeName>Hassane</ForeName>
<Initials>H</Initials>
<AffiliationInfo>
<Affiliation>Saint Joseph University Hôtel-Dieu de France, Beirut, Lebanon.</Affiliation>
</AffiliationInfo>
</Author>
<Author ValidYN="Y">
<LastName>Bombardier</LastName>
<ForeName>Claire</ForeName>
<Initials>C</Initials>
<AffiliationInfo>
<Affiliation>University of Toronto, Toronto General Research Institute, Institute for Work and Health, and Mount Sinai Hospital, Toronto, Ontario, Canada.</Affiliation>
</AffiliationInfo>
</Author>
<Author ValidYN="Y">
<LastName>Hajjaj-Hassouni</LastName>
<ForeName>Najia</ForeName>
<Initials>N</Initials>
<AffiliationInfo>
<Affiliation>Mohammed Vth Souissi University, CNRST, and Laboratory of Information and Research on Bone Diseases (LIRPOS-URAC 30), Rabat, Morocco, and El Ayachi Hospital and University Hospital, Salé, Morocco.</Affiliation>
</AffiliationInfo>
</Author>
<Author ValidYN="Y">
<LastName>Logeart</LastName>
<ForeName>Isabelle</ForeName>
<Initials>I</Initials>
<AffiliationInfo>
<Affiliation>Pfizer, Paris, France.</Affiliation>
</AffiliationInfo>
</Author>
<Author ValidYN="Y">
<LastName>Matucci-Cerinic</LastName>
<ForeName>Marco</ForeName>
<Initials>M</Initials>
<AffiliationInfo>
<Affiliation>Denothe Centre, University of Florence, Florence, Italy.</Affiliation>
</AffiliationInfo>
</Author>
<Author ValidYN="Y">
<LastName>van de Laar</LastName>
<ForeName>Mart</ForeName>
<Initials>M</Initials>
<AffiliationInfo>
<Affiliation>Arthritis Center Twente, Medisch Spectrum Twente, and University Twente, Enschede, The Netherlands.</Affiliation>
</AffiliationInfo>
</Author>
<Author ValidYN="Y">
<LastName>van der Heijde</LastName>
<ForeName>Désirée</ForeName>
<Initials>D</Initials>
<AffiliationInfo>
<Affiliation>Leiden University Medical Center, Leiden, The Netherlands.</Affiliation>
</AffiliationInfo>
</Author>
<Author ValidYN="Y">
<LastName>Dougados</LastName>
<ForeName>Maxime</ForeName>
<Initials>M</Initials>
<AffiliationInfo>
<Affiliation>Paris Descartes University, Cochin Hospital, AP-HP, INSERM (U1153), PRES Sorbonne Paris-Cité, Paris, France.</Affiliation>
</AffiliationInfo>
</Author>
</AuthorList>
<Language>eng</Language>
<PublicationTypeList>
<PublicationType UI="D016428">Journal Article</PublicationType>
<PublicationType UI="D064888">Observational Study</PublicationType>
<PublicationType UI="D013485">Research Support, Non-U.S. Gov't</PublicationType>
</PublicationTypeList>
</Article>
<MedlineJournalInfo>
<Country>United States</Country>
<MedlineTA>Arthritis Care Res (Hoboken)</MedlineTA>
<NlmUniqueID>101518086</NlmUniqueID>
<ISSNLinking>2151-464X</ISSNLinking>
</MedlineJournalInfo>
<ChemicalList>
<Chemical>
<RegistryNumber>0</RegistryNumber>
<NameOfSubstance UI="D000894">Anti-Inflammatory Agents, Non-Steroidal</NameOfSubstance>
</Chemical>
</ChemicalList>
<CitationSubset>IM</CitationSubset>
<MeshHeadingList>
<MeshHeading>
<DescriptorName UI="D000894" MajorTopicYN="N">Anti-Inflammatory Agents, Non-Steroidal</DescriptorName>
<QualifierName UI="Q000627" MajorTopicYN="N">therapeutic use</QualifierName>
</MeshHeading>
<MeshHeading>
<DescriptorName UI="D001315" MajorTopicYN="N" Type="Geographic">Australia</DescriptorName>
<QualifierName UI="Q000453" MajorTopicYN="N">epidemiology</QualifierName>
</MeshHeading>
<MeshHeading>
<DescriptorName UI="D005060" MajorTopicYN="N" Type="Geographic">Europe</DescriptorName>
<QualifierName UI="Q000453" MajorTopicYN="N">epidemiology</QualifierName>
</MeshHeading>
<MeshHeading>
<DescriptorName UI="D005260" MajorTopicYN="N">Female</DescriptorName>
</MeshHeading>
<MeshHeading>
<DescriptorName UI="D006801" MajorTopicYN="N">Humans</DescriptorName>
</MeshHeading>
<MeshHeading>
<DescriptorName UI="D038622" MajorTopicYN="Y">Internationality</DescriptorName>
</MeshHeading>
<MeshHeading>
<DescriptorName UI="D007861" MajorTopicYN="N" Type="Geographic">Lebanon</DescriptorName>
<QualifierName UI="Q000453" MajorTopicYN="N">epidemiology</QualifierName>
</MeshHeading>
<MeshHeading>
<DescriptorName UI="D008137" MajorTopicYN="N">Longitudinal Studies</DescriptorName>
</MeshHeading>
<MeshHeading>
<DescriptorName UI="D008297" MajorTopicYN="N">Male</DescriptorName>
</MeshHeading>
<MeshHeading>
<DescriptorName UI="D009018" MajorTopicYN="N" Type="Geographic">Morocco</DescriptorName>
<QualifierName UI="Q000453" MajorTopicYN="N">epidemiology</QualifierName>
</MeshHeading>
<MeshHeading>
<DescriptorName UI="D010003" MajorTopicYN="N">Osteoarthritis</DescriptorName>
<QualifierName UI="Q000175" MajorTopicYN="Y">diagnosis</QualifierName>
<QualifierName UI="Q000453" MajorTopicYN="N">epidemiology</QualifierName>
<QualifierName UI="Q000628" MajorTopicYN="Y">therapy</QualifierName>
</MeshHeading>
<MeshHeading>
<DescriptorName UI="D010147" MajorTopicYN="N">Pain Measurement</DescriptorName>
<QualifierName UI="Q000379" MajorTopicYN="N">methods</QualifierName>
<QualifierName UI="Q000592" MajorTopicYN="Y">standards</QualifierName>
</MeshHeading>
<MeshHeading>
<DescriptorName UI="D017060" MajorTopicYN="Y">Patient Satisfaction</DescriptorName>
</MeshHeading>
<MeshHeading>
<DescriptorName UI="D011446" MajorTopicYN="N">Prospective Studies</DescriptorName>
</MeshHeading>
<MeshHeading>
<DescriptorName UI="D016896" MajorTopicYN="N">Treatment Outcome</DescriptorName>
</MeshHeading>
</MeshHeadingList>
</MedlineCitation>
<PubmedData>
<History>
<PubMedPubDate PubStatus="received">
<Year>2014</Year>
<Month>07</Month>
<Day>17</Day>
</PubMedPubDate>
<PubMedPubDate PubStatus="revised">
<Year>2014</Year>
<Month>11</Month>
<Day>03</Day>
</PubMedPubDate>
<PubMedPubDate PubStatus="accepted">
<Year>2014</Year>
<Month>12</Month>
<Day>16</Day>
</PubMedPubDate>
<PubMedPubDate PubStatus="entrez">
<Year>2015</Year>
<Month>1</Month>
<Day>13</Day>
<Hour>6</Hour>
<Minute>0</Minute>
</PubMedPubDate>
<PubMedPubDate PubStatus="pubmed">
<Year>2015</Year>
<Month>1</Month>
<Day>13</Day>
<Hour>6</Hour>
<Minute>0</Minute>
</PubMedPubDate>
<PubMedPubDate PubStatus="medline">
<Year>2015</Year>
<Month>9</Month>
<Day>10</Day>
<Hour>6</Hour>
<Minute>0</Minute>
</PubMedPubDate>
</History>
<PublicationStatus>ppublish</PublicationStatus>
<ArticleIdList>
<ArticleId IdType="pubmed">25581339</ArticleId>
<ArticleId IdType="doi">10.1002/acr.22538</ArticleId>
</ArticleIdList>
</PubmedData>
</pubmed>
<affiliations>
<list>
<country>
<li>Australie</li>
<li>Canada</li>
<li>Espagne</li>
<li>France</li>
<li>Italie</li>
<li>Liban</li>
<li>Maroc</li>
<li>Pays-Bas</li>
<li>États-Unis</li>
</country>
<region>
<li>Communauté de Madrid</li>
<li>Hollande-Méridionale</li>
<li>Maryland</li>
<li>Ontario</li>
<li>Île-de-France</li>
</region>
<settlement>
<li>Baltimore</li>
<li>Leyde</li>
<li>Madrid</li>
<li>Paris</li>
<li>Toronto</li>
</settlement>
<orgName>
<li>Université de Toronto</li>
</orgName>
</list>
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<country name="Australie">
<noRegion>
<name sortKey="Bellamy, Nicholas" sort="Bellamy, Nicholas" uniqKey="Bellamy N" first="Nicholas" last="Bellamy">Nicholas Bellamy</name>
</noRegion>
</country>
<country name="États-Unis">
<region name="Maryland">
<name sortKey="Hochberg, Marc" sort="Hochberg, Marc" uniqKey="Hochberg M" first="Marc" last="Hochberg">Marc Hochberg</name>
</region>
</country>
<country name="France">
<region name="Île-de-France">
<name sortKey="Tubach, Florence" sort="Tubach, Florence" uniqKey="Tubach F" first="Florence" last="Tubach">Florence Tubach</name>
</region>
<name sortKey="Dougados, Maxime" sort="Dougados, Maxime" uniqKey="Dougados M" first="Maxime" last="Dougados">Maxime Dougados</name>
<name sortKey="Logeart, Isabelle" sort="Logeart, Isabelle" uniqKey="Logeart I" first="Isabelle" last="Logeart">Isabelle Logeart</name>
</country>
<country name="Espagne">
<region name="Communauté de Madrid">
<name sortKey="Martin Mola, Emilio" sort="Martin Mola, Emilio" uniqKey="Martin Mola E" first="Emilio" last="Martin-Mola">Emilio Martin-Mola</name>
</region>
</country>
<country name="Liban">
<noRegion>
<name sortKey="Awada, Hassane" sort="Awada, Hassane" uniqKey="Awada H" first="Hassane" last="Awada">Hassane Awada</name>
</noRegion>
</country>
<country name="Canada">
<region name="Ontario">
<name sortKey="Bombardier, Claire" sort="Bombardier, Claire" uniqKey="Bombardier C" first="Claire" last="Bombardier">Claire Bombardier</name>
</region>
</country>
<country name="Maroc">
<noRegion>
<name sortKey="Hajjaj Hassouni, Najia" sort="Hajjaj Hassouni, Najia" uniqKey="Hajjaj Hassouni N" first="Najia" last="Hajjaj-Hassouni">Najia Hajjaj-Hassouni</name>
</noRegion>
</country>
<country name="Italie">
<noRegion>
<name sortKey="Matucci Cerinic, Marco" sort="Matucci Cerinic, Marco" uniqKey="Matucci Cerinic M" first="Marco" last="Matucci-Cerinic">Marco Matucci-Cerinic</name>
</noRegion>
</country>
<country name="Pays-Bas">
<noRegion>
<name sortKey="Van De Laar, Mart" sort="Van De Laar, Mart" uniqKey="Van De Laar M" first="Mart" last="Van De Laar">Mart Van De Laar</name>
</noRegion>
<name sortKey="Van Der Heijde, Desiree" sort="Van Der Heijde, Desiree" uniqKey="Van Der Heijde D" first="Désirée" last="Van Der Heijde">Désirée Van Der Heijde</name>
</country>
</tree>
</affiliations>
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