Serveur d'exploration sur les relations entre la France et l'Australie

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Erratum to: An exploratory randomised double-blind and placebo-controlled phase 2 study of a combination of baclofen, naltrexone and sorbitol (PXT3003) in patients with Charcot-Marie-Tooth disease type 1A

Identifieur interne : 000942 ( Pmc/Curation ); précédent : 000941; suivant : 000943

Erratum to: An exploratory randomised double-blind and placebo-controlled phase 2 study of a combination of baclofen, naltrexone and sorbitol (PXT3003) in patients with Charcot-Marie-Tooth disease type 1A

Auteurs : Shahram Attarian [France] ; Jean-Michel Vallat [France] ; Laurent Magy [France] ; Benoît Funalot [France] ; Pierre-Marie Gonnaud [France] ; Arnaud Lacour [France] ; Yann Péréon [France] ; Odile Dubourg [France] ; Jean Pouget [France] ; Joëlle Micallef [France] ; Jérôme Franques [France] ; Marie-Noëlle Lefebvre [France] ; Karima Ghorab [France] ; Mahmoud Al-Moussawi [France] ; Vincent Tiffreau [France] ; Marguerite Preudhomme [France] ; Armelle Magot [France] ; Laurène Leclair-Visonneau [France] ; Tanya Stojkovic [France] ; Laura Bossi [France] ; Philippe Lehert [Australie, Belgique] ; Walter Gilbert [États-Unis] ; Viviane Bertrand [France] ; Jonas Mandel [France] ; Aude Milet [France] ; Rodolphe Hajj [France] ; Lamia Boudiaf [France] ; Catherine Scart-Grès [France] ; Serguei Nabirotchkin [France] ; Mickael Guedj [France] ; Ilya Chumakov [France] ; Daniel Cohen [France]

Source :

RBID : PMC:4937550
Url:
DOI: 10.1186/s13023-016-0463-6
PubMed: 27387831
PubMed Central: 4937550

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PMC:4937550

Le document en format XML

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<title xml:lang="en">Erratum to: An exploratory randomised double-blind and placebo-controlled phase 2 study of a combination of baclofen, naltrexone and sorbitol (PXT3003) in patients with Charcot-Marie-Tooth disease type 1A</title>
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<name sortKey="Pereon, Yann" sort="Pereon, Yann" uniqKey="Pereon Y" first="Yann" last="Péréon">Yann Péréon</name>
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<name sortKey="Dubourg, Odile" sort="Dubourg, Odile" uniqKey="Dubourg O" first="Odile" last="Dubourg">Odile Dubourg</name>
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<nlm:aff id="Aff7">CHU de Paris - Groupe Hospitalier Pitié-Salpétrière, 47-83 boulevard de l’Hôpital, 75013 Paris, France</nlm:aff>
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<name sortKey="Pouget, Jean" sort="Pouget, Jean" uniqKey="Pouget J" first="Jean" last="Pouget">Jean Pouget</name>
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<name sortKey="Micallef, Joelle" sort="Micallef, Joelle" uniqKey="Micallef J" first="Joëlle" last="Micallef">Joëlle Micallef</name>
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<name sortKey="Franques, Jerome" sort="Franques, Jerome" uniqKey="Franques J" first="Jérôme" last="Franques">Jérôme Franques</name>
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<name sortKey="Lefebvre, Marie Noelle" sort="Lefebvre, Marie Noelle" uniqKey="Lefebvre M" first="Marie-Noëlle" last="Lefebvre">Marie-Noëlle Lefebvre</name>
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<name sortKey="Ghorab, Karima" sort="Ghorab, Karima" uniqKey="Ghorab K" first="Karima" last="Ghorab">Karima Ghorab</name>
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<name sortKey="Al Moussawi, Mahmoud" sort="Al Moussawi, Mahmoud" uniqKey="Al Moussawi M" first="Mahmoud" last="Al-Moussawi">Mahmoud Al-Moussawi</name>
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<name sortKey="Tiffreau, Vincent" sort="Tiffreau, Vincent" uniqKey="Tiffreau V" first="Vincent" last="Tiffreau">Vincent Tiffreau</name>
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<name sortKey="Preudhomme, Marguerite" sort="Preudhomme, Marguerite" uniqKey="Preudhomme M" first="Marguerite" last="Preudhomme">Marguerite Preudhomme</name>
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<name sortKey="Magot, Armelle" sort="Magot, Armelle" uniqKey="Magot A" first="Armelle" last="Magot">Armelle Magot</name>
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<name sortKey="Leclair Visonneau, Laurene" sort="Leclair Visonneau, Laurene" uniqKey="Leclair Visonneau L" first="Laurène" last="Leclair-Visonneau">Laurène Leclair-Visonneau</name>
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<name sortKey="Stojkovic, Tanya" sort="Stojkovic, Tanya" uniqKey="Stojkovic T" first="Tanya" last="Stojkovic">Tanya Stojkovic</name>
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<name sortKey="Bossi, Laura" sort="Bossi, Laura" uniqKey="Bossi L" first="Laura" last="Bossi">Laura Bossi</name>
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<nlm:aff id="Aff8">Admissions, 75017 Paris, France</nlm:aff>
<country xml:lang="fr">France</country>
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<name sortKey="Lehert, Philippe" sort="Lehert, Philippe" uniqKey="Lehert P" first="Philippe" last="Lehert">Philippe Lehert</name>
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<nlm:aff id="Aff10">Faculty of Economics, UCL Mons, Louvain, Belgium</nlm:aff>
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<name sortKey="Gilbert, Walter" sort="Gilbert, Walter" uniqKey="Gilbert W" first="Walter" last="Gilbert">Walter Gilbert</name>
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<nlm:aff id="Aff11">Carl M. Loeb University Professor Emeritus, Harvard University, Cambridge, MA 02138 USA</nlm:aff>
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<region type="state">Massachusetts</region>
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<wicri:cityArea>Carl M. Loeb University Professor Emeritus, Harvard University, Cambridge</wicri:cityArea>
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<name sortKey="Bertrand, Viviane" sort="Bertrand, Viviane" uniqKey="Bertrand V" first="Viviane" last="Bertrand">Viviane Bertrand</name>
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<nlm:aff id="Aff12">Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris, France</nlm:aff>
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<name sortKey="Mandel, Jonas" sort="Mandel, Jonas" uniqKey="Mandel J" first="Jonas" last="Mandel">Jonas Mandel</name>
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<nlm:aff id="Aff12">Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris, France</nlm:aff>
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<name sortKey="Milet, Aude" sort="Milet, Aude" uniqKey="Milet A" first="Aude" last="Milet">Aude Milet</name>
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<name sortKey="Hajj, Rodolphe" sort="Hajj, Rodolphe" uniqKey="Hajj R" first="Rodolphe" last="Hajj">Rodolphe Hajj</name>
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<name sortKey="Boudiaf, Lamia" sort="Boudiaf, Lamia" uniqKey="Boudiaf L" first="Lamia" last="Boudiaf">Lamia Boudiaf</name>
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<name sortKey="Scart Gres, Catherine" sort="Scart Gres, Catherine" uniqKey="Scart Gres C" first="Catherine" last="Scart-Grès">Catherine Scart-Grès</name>
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<name sortKey="Nabirotchkin, Serguei" sort="Nabirotchkin, Serguei" uniqKey="Nabirotchkin S" first="Serguei" last="Nabirotchkin">Serguei Nabirotchkin</name>
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<name sortKey="Guedj, Mickael" sort="Guedj, Mickael" uniqKey="Guedj M" first="Mickael" last="Guedj">Mickael Guedj</name>
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<name sortKey="Chumakov, Ilya" sort="Chumakov, Ilya" uniqKey="Chumakov I" first="Ilya" last="Chumakov">Ilya Chumakov</name>
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<name sortKey="Cohen, Daniel" sort="Cohen, Daniel" uniqKey="Cohen D" first="Daniel" last="Cohen">Daniel Cohen</name>
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<title xml:lang="en" level="a" type="main">Erratum to: An exploratory randomised double-blind and placebo-controlled phase 2 study of a combination of baclofen, naltrexone and sorbitol (PXT3003) in patients with Charcot-Marie-Tooth disease type 1A</title>
<author>
<name sortKey="Attarian, Shahram" sort="Attarian, Shahram" uniqKey="Attarian S" first="Shahram" last="Attarian">Shahram Attarian</name>
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<name sortKey="Vallat, Jean Michel" sort="Vallat, Jean Michel" uniqKey="Vallat J" first="Jean-Michel" last="Vallat">Jean-Michel Vallat</name>
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<name sortKey="Magy, Laurent" sort="Magy, Laurent" uniqKey="Magy L" first="Laurent" last="Magy">Laurent Magy</name>
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<nlm:aff id="Aff3">CHU de Limoges - Hôpital Dupuytren, 2 Avenue Martin Luther King, 87042 Limoges, France</nlm:aff>
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<name sortKey="Funalot, Benoit" sort="Funalot, Benoit" uniqKey="Funalot B" first="Benoît" last="Funalot">Benoît Funalot</name>
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<nlm:aff id="Aff3">CHU de Limoges - Hôpital Dupuytren, 2 Avenue Martin Luther King, 87042 Limoges, France</nlm:aff>
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<name sortKey="Gonnaud, Pierre Marie" sort="Gonnaud, Pierre Marie" uniqKey="Gonnaud P" first="Pierre-Marie" last="Gonnaud">Pierre-Marie Gonnaud</name>
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<name sortKey="Lacour, Arnaud" sort="Lacour, Arnaud" uniqKey="Lacour A" first="Arnaud" last="Lacour">Arnaud Lacour</name>
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<nlm:aff id="Aff5">CHRU de Lille - Hôpital Roger Salengro, rue Emile Laine, 59037 Lille, France</nlm:aff>
<country xml:lang="fr">France</country>
<wicri:regionArea>CHRU de Lille - Hôpital Roger Salengro, rue Emile Laine, 59037 Lille</wicri:regionArea>
</affiliation>
</author>
<author>
<name sortKey="Pereon, Yann" sort="Pereon, Yann" uniqKey="Pereon Y" first="Yann" last="Péréon">Yann Péréon</name>
<affiliation wicri:level="1">
<nlm:aff id="Aff6">CHU de Nantes - Hôtel Dieu, 1 place Alexis Ricordeau, 44093 Nantes, France</nlm:aff>
<country xml:lang="fr">France</country>
<wicri:regionArea>CHU de Nantes - Hôtel Dieu, 1 place Alexis Ricordeau, 44093 Nantes</wicri:regionArea>
</affiliation>
</author>
<author>
<name sortKey="Dubourg, Odile" sort="Dubourg, Odile" uniqKey="Dubourg O" first="Odile" last="Dubourg">Odile Dubourg</name>
<affiliation wicri:level="1">
<nlm:aff id="Aff7">CHU de Paris - Groupe Hospitalier Pitié-Salpétrière, 47-83 boulevard de l’Hôpital, 75013 Paris, France</nlm:aff>
<country xml:lang="fr">France</country>
<wicri:regionArea>CHU de Paris - Groupe Hospitalier Pitié-Salpétrière, 47-83 boulevard de l’Hôpital, 75013 Paris</wicri:regionArea>
</affiliation>
</author>
<author>
<name sortKey="Pouget, Jean" sort="Pouget, Jean" uniqKey="Pouget J" first="Jean" last="Pouget">Jean Pouget</name>
<affiliation wicri:level="1">
<nlm:aff id="Aff1">Centre de référence des maladies neuromusculaires et de la SLA, Pôle des neurosciences Cliniques, AP-HM et Aix Marseille Université, Marseille, France</nlm:aff>
<country xml:lang="fr">France</country>
<wicri:regionArea>Centre de référence des maladies neuromusculaires et de la SLA, Pôle des neurosciences Cliniques, AP-HM et Aix Marseille Université, Marseille</wicri:regionArea>
</affiliation>
</author>
<author>
<name sortKey="Micallef, Joelle" sort="Micallef, Joelle" uniqKey="Micallef J" first="Joëlle" last="Micallef">Joëlle Micallef</name>
<affiliation wicri:level="1">
<nlm:aff id="Aff2">CIC-Centre de Pharmacologie Clinique et D’Evaluations Therapeutiques, AP-HM et Aix Marseille Université, Marseille, France</nlm:aff>
<country xml:lang="fr">France</country>
<wicri:regionArea>CIC-Centre de Pharmacologie Clinique et D’Evaluations Therapeutiques, AP-HM et Aix Marseille Université, Marseille</wicri:regionArea>
</affiliation>
</author>
<author>
<name sortKey="Franques, Jerome" sort="Franques, Jerome" uniqKey="Franques J" first="Jérôme" last="Franques">Jérôme Franques</name>
<affiliation wicri:level="1">
<nlm:aff id="Aff1">Centre de référence des maladies neuromusculaires et de la SLA, Pôle des neurosciences Cliniques, AP-HM et Aix Marseille Université, Marseille, France</nlm:aff>
<country xml:lang="fr">France</country>
<wicri:regionArea>Centre de référence des maladies neuromusculaires et de la SLA, Pôle des neurosciences Cliniques, AP-HM et Aix Marseille Université, Marseille</wicri:regionArea>
</affiliation>
</author>
<author>
<name sortKey="Lefebvre, Marie Noelle" sort="Lefebvre, Marie Noelle" uniqKey="Lefebvre M" first="Marie-Noëlle" last="Lefebvre">Marie-Noëlle Lefebvre</name>
<affiliation wicri:level="1">
<nlm:aff id="Aff2">CIC-Centre de Pharmacologie Clinique et D’Evaluations Therapeutiques, AP-HM et Aix Marseille Université, Marseille, France</nlm:aff>
<country xml:lang="fr">France</country>
<wicri:regionArea>CIC-Centre de Pharmacologie Clinique et D’Evaluations Therapeutiques, AP-HM et Aix Marseille Université, Marseille</wicri:regionArea>
</affiliation>
</author>
<author>
<name sortKey="Ghorab, Karima" sort="Ghorab, Karima" uniqKey="Ghorab K" first="Karima" last="Ghorab">Karima Ghorab</name>
<affiliation wicri:level="1">
<nlm:aff id="Aff3">CHU de Limoges - Hôpital Dupuytren, 2 Avenue Martin Luther King, 87042 Limoges, France</nlm:aff>
<country xml:lang="fr">France</country>
<wicri:regionArea>CHU de Limoges - Hôpital Dupuytren, 2 Avenue Martin Luther King, 87042 Limoges</wicri:regionArea>
</affiliation>
</author>
<author>
<name sortKey="Al Moussawi, Mahmoud" sort="Al Moussawi, Mahmoud" uniqKey="Al Moussawi M" first="Mahmoud" last="Al-Moussawi">Mahmoud Al-Moussawi</name>
<affiliation wicri:level="1">
<nlm:aff id="Aff4">CHU Lyon Sud, 165 Chemin du Grand Revoyet, 69495 Lyon, France</nlm:aff>
<country xml:lang="fr">France</country>
<wicri:regionArea>CHU Lyon Sud, 165 Chemin du Grand Revoyet, 69495 Lyon</wicri:regionArea>
</affiliation>
</author>
<author>
<name sortKey="Tiffreau, Vincent" sort="Tiffreau, Vincent" uniqKey="Tiffreau V" first="Vincent" last="Tiffreau">Vincent Tiffreau</name>
<affiliation wicri:level="1">
<nlm:aff id="Aff5">CHRU de Lille - Hôpital Roger Salengro, rue Emile Laine, 59037 Lille, France</nlm:aff>
<country xml:lang="fr">France</country>
<wicri:regionArea>CHRU de Lille - Hôpital Roger Salengro, rue Emile Laine, 59037 Lille</wicri:regionArea>
</affiliation>
</author>
<author>
<name sortKey="Preudhomme, Marguerite" sort="Preudhomme, Marguerite" uniqKey="Preudhomme M" first="Marguerite" last="Preudhomme">Marguerite Preudhomme</name>
<affiliation wicri:level="1">
<nlm:aff id="Aff5">CHRU de Lille - Hôpital Roger Salengro, rue Emile Laine, 59037 Lille, France</nlm:aff>
<country xml:lang="fr">France</country>
<wicri:regionArea>CHRU de Lille - Hôpital Roger Salengro, rue Emile Laine, 59037 Lille</wicri:regionArea>
</affiliation>
</author>
<author>
<name sortKey="Magot, Armelle" sort="Magot, Armelle" uniqKey="Magot A" first="Armelle" last="Magot">Armelle Magot</name>
<affiliation wicri:level="1">
<nlm:aff id="Aff6">CHU de Nantes - Hôtel Dieu, 1 place Alexis Ricordeau, 44093 Nantes, France</nlm:aff>
<country xml:lang="fr">France</country>
<wicri:regionArea>CHU de Nantes - Hôtel Dieu, 1 place Alexis Ricordeau, 44093 Nantes</wicri:regionArea>
</affiliation>
</author>
<author>
<name sortKey="Leclair Visonneau, Laurene" sort="Leclair Visonneau, Laurene" uniqKey="Leclair Visonneau L" first="Laurène" last="Leclair-Visonneau">Laurène Leclair-Visonneau</name>
<affiliation wicri:level="1">
<nlm:aff id="Aff5">CHRU de Lille - Hôpital Roger Salengro, rue Emile Laine, 59037 Lille, France</nlm:aff>
<country xml:lang="fr">France</country>
<wicri:regionArea>CHRU de Lille - Hôpital Roger Salengro, rue Emile Laine, 59037 Lille</wicri:regionArea>
</affiliation>
</author>
<author>
<name sortKey="Stojkovic, Tanya" sort="Stojkovic, Tanya" uniqKey="Stojkovic T" first="Tanya" last="Stojkovic">Tanya Stojkovic</name>
<affiliation wicri:level="1">
<nlm:aff id="Aff7">CHU de Paris - Groupe Hospitalier Pitié-Salpétrière, 47-83 boulevard de l’Hôpital, 75013 Paris, France</nlm:aff>
<country xml:lang="fr">France</country>
<wicri:regionArea>CHU de Paris - Groupe Hospitalier Pitié-Salpétrière, 47-83 boulevard de l’Hôpital, 75013 Paris</wicri:regionArea>
</affiliation>
</author>
<author>
<name sortKey="Bossi, Laura" sort="Bossi, Laura" uniqKey="Bossi L" first="Laura" last="Bossi">Laura Bossi</name>
<affiliation wicri:level="1">
<nlm:aff id="Aff8">Admissions, 75017 Paris, France</nlm:aff>
<country xml:lang="fr">France</country>
<wicri:regionArea>Admissions, 75017 Paris</wicri:regionArea>
</affiliation>
</author>
<author>
<name sortKey="Lehert, Philippe" sort="Lehert, Philippe" uniqKey="Lehert P" first="Philippe" last="Lehert">Philippe Lehert</name>
<affiliation wicri:level="4">
<nlm:aff id="Aff9">Faculty of Medicine, The University of Melbourne, Grattan St, Melbourne, VIC 3010 Australia</nlm:aff>
<orgName type="university">Université de Melbourne</orgName>
<country>Australie</country>
<placeName>
<settlement type="city">Melbourne</settlement>
<region type="état">Victoria (État)</region>
</placeName>
</affiliation>
<affiliation wicri:level="1">
<nlm:aff id="Aff10">Faculty of Economics, UCL Mons, Louvain, Belgium</nlm:aff>
<country xml:lang="fr">Belgique</country>
<wicri:regionArea>Faculty of Economics, UCL Mons, Louvain</wicri:regionArea>
</affiliation>
</author>
<author>
<name sortKey="Gilbert, Walter" sort="Gilbert, Walter" uniqKey="Gilbert W" first="Walter" last="Gilbert">Walter Gilbert</name>
<affiliation wicri:level="2">
<nlm:aff id="Aff11">Carl M. Loeb University Professor Emeritus, Harvard University, Cambridge, MA 02138 USA</nlm:aff>
<country xml:lang="fr">États-Unis</country>
<placeName>
<region type="state">Massachusetts</region>
</placeName>
<wicri:cityArea>Carl M. Loeb University Professor Emeritus, Harvard University, Cambridge</wicri:cityArea>
</affiliation>
</author>
<author>
<name sortKey="Bertrand, Viviane" sort="Bertrand, Viviane" uniqKey="Bertrand V" first="Viviane" last="Bertrand">Viviane Bertrand</name>
<affiliation wicri:level="1">
<nlm:aff id="Aff12">Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris, France</nlm:aff>
<country xml:lang="fr">France</country>
<wicri:regionArea>Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris</wicri:regionArea>
</affiliation>
</author>
<author>
<name sortKey="Mandel, Jonas" sort="Mandel, Jonas" uniqKey="Mandel J" first="Jonas" last="Mandel">Jonas Mandel</name>
<affiliation wicri:level="1">
<nlm:aff id="Aff12">Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris, France</nlm:aff>
<country xml:lang="fr">France</country>
<wicri:regionArea>Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris</wicri:regionArea>
</affiliation>
</author>
<author>
<name sortKey="Milet, Aude" sort="Milet, Aude" uniqKey="Milet A" first="Aude" last="Milet">Aude Milet</name>
<affiliation wicri:level="1">
<nlm:aff id="Aff12">Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris, France</nlm:aff>
<country xml:lang="fr">France</country>
<wicri:regionArea>Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris</wicri:regionArea>
</affiliation>
</author>
<author>
<name sortKey="Hajj, Rodolphe" sort="Hajj, Rodolphe" uniqKey="Hajj R" first="Rodolphe" last="Hajj">Rodolphe Hajj</name>
<affiliation wicri:level="1">
<nlm:aff id="Aff12">Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris, France</nlm:aff>
<country xml:lang="fr">France</country>
<wicri:regionArea>Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris</wicri:regionArea>
</affiliation>
</author>
<author>
<name sortKey="Boudiaf, Lamia" sort="Boudiaf, Lamia" uniqKey="Boudiaf L" first="Lamia" last="Boudiaf">Lamia Boudiaf</name>
<affiliation wicri:level="1">
<nlm:aff id="Aff12">Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris, France</nlm:aff>
<country xml:lang="fr">France</country>
<wicri:regionArea>Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris</wicri:regionArea>
</affiliation>
</author>
<author>
<name sortKey="Scart Gres, Catherine" sort="Scart Gres, Catherine" uniqKey="Scart Gres C" first="Catherine" last="Scart-Grès">Catherine Scart-Grès</name>
<affiliation wicri:level="1">
<nlm:aff id="Aff12">Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris, France</nlm:aff>
<country xml:lang="fr">France</country>
<wicri:regionArea>Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris</wicri:regionArea>
</affiliation>
</author>
<author>
<name sortKey="Nabirotchkin, Serguei" sort="Nabirotchkin, Serguei" uniqKey="Nabirotchkin S" first="Serguei" last="Nabirotchkin">Serguei Nabirotchkin</name>
<affiliation wicri:level="1">
<nlm:aff id="Aff12">Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris, France</nlm:aff>
<country xml:lang="fr">France</country>
<wicri:regionArea>Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris</wicri:regionArea>
</affiliation>
</author>
<author>
<name sortKey="Guedj, Mickael" sort="Guedj, Mickael" uniqKey="Guedj M" first="Mickael" last="Guedj">Mickael Guedj</name>
<affiliation wicri:level="1">
<nlm:aff id="Aff12">Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris, France</nlm:aff>
<country xml:lang="fr">France</country>
<wicri:regionArea>Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris</wicri:regionArea>
</affiliation>
</author>
<author>
<name sortKey="Chumakov, Ilya" sort="Chumakov, Ilya" uniqKey="Chumakov I" first="Ilya" last="Chumakov">Ilya Chumakov</name>
<affiliation wicri:level="1">
<nlm:aff id="Aff12">Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris, France</nlm:aff>
<country xml:lang="fr">France</country>
<wicri:regionArea>Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris</wicri:regionArea>
</affiliation>
</author>
<author>
<name sortKey="Cohen, Daniel" sort="Cohen, Daniel" uniqKey="Cohen D" first="Daniel" last="Cohen">Daniel Cohen</name>
<affiliation wicri:level="1">
<nlm:aff id="Aff12">Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris, France</nlm:aff>
<country xml:lang="fr">France</country>
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<series>
<title level="j">Orphanet Journal of Rare Diseases</title>
<idno type="eISSN">1750-1172</idno>
<imprint>
<date when="2016">2016</date>
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<analytic>
<author>
<name sortKey="Attarian, S" uniqKey="Attarian S">S Attarian</name>
</author>
<author>
<name sortKey="Vallat, Jm" uniqKey="Vallat J">JM Vallat</name>
</author>
<author>
<name sortKey="Magy, L" uniqKey="Magy L">L Magy</name>
</author>
<author>
<name sortKey="Funalot, B" uniqKey="Funalot B">B Funalot</name>
</author>
<author>
<name sortKey="Gonnaud, Pm" uniqKey="Gonnaud P">PM Gonnaud</name>
</author>
<author>
<name sortKey="Lacour, A" uniqKey="Lacour A">A Lacour</name>
</author>
<author>
<name sortKey="Pereon, Y" uniqKey="Pereon Y">Y Péréon</name>
</author>
<author>
<name sortKey="Dubourg, O" uniqKey="Dubourg O">O Dubourg</name>
</author>
<author>
<name sortKey="Pouget, J" uniqKey="Pouget J">J Pouget</name>
</author>
<author>
<name sortKey="Micallef, J" uniqKey="Micallef J">J Micallef</name>
</author>
<author>
<name sortKey="Franques, J" uniqKey="Franques J">J Franques</name>
</author>
<author>
<name sortKey="Lefebvre, Mn" uniqKey="Lefebvre M">MN Lefebvre</name>
</author>
<author>
<name sortKey="Ghorab, K" uniqKey="Ghorab K">K Ghorab</name>
</author>
<author>
<name sortKey="Al Moussawi, M" uniqKey="Al Moussawi M">M Al-Moussawi</name>
</author>
<author>
<name sortKey="Tiffreau, V" uniqKey="Tiffreau V">V Tiffreau</name>
</author>
<author>
<name sortKey="Preudhomme, M" uniqKey="Preudhomme M">M Preudhomme</name>
</author>
<author>
<name sortKey="Magot, A" uniqKey="Magot A">A Magot</name>
</author>
<author>
<name sortKey="Leclair Visonneau, L" uniqKey="Leclair Visonneau L">L Leclair-Visonneau</name>
</author>
<author>
<name sortKey="Stojkovic, T" uniqKey="Stojkovic T">T Stojkovic</name>
</author>
<author>
<name sortKey="Bossi, L" uniqKey="Bossi L">L Bossi</name>
</author>
<author>
<name sortKey="Lehert, P" uniqKey="Lehert P">P Lehert</name>
</author>
<author>
<name sortKey="Gilbert, W" uniqKey="Gilbert W">W Gilbert</name>
</author>
<author>
<name sortKey="Bertrand, V" uniqKey="Bertrand V">V Bertrand</name>
</author>
<author>
<name sortKey="Mandel, J" uniqKey="Mandel J">J Mandel</name>
</author>
<author>
<name sortKey="Milet, A" uniqKey="Milet A">A Milet</name>
</author>
<author>
<name sortKey="Hajj, R" uniqKey="Hajj R">R Hajj</name>
</author>
<author>
<name sortKey="Boudiaf, L" uniqKey="Boudiaf L">L Boudiaf</name>
</author>
<author>
<name sortKey="Scart Gres, C" uniqKey="Scart Gres C">C Scart-Grès</name>
</author>
<author>
<name sortKey="Nabirotchkin, S" uniqKey="Nabirotchkin S">S Nabirotchkin</name>
</author>
<author>
<name sortKey="Guedj, M" uniqKey="Guedj M">M Guedj</name>
</author>
<author>
<name sortKey="Chumakov, I" uniqKey="Chumakov I">I Chumakov</name>
</author>
<author>
<name sortKey="Cohen, D" uniqKey="Cohen D">D Cohen</name>
</author>
</analytic>
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<journal-id journal-id-type="nlm-ta">Orphanet J Rare Dis</journal-id>
<journal-id journal-id-type="iso-abbrev">Orphanet J Rare Dis</journal-id>
<journal-title-group>
<journal-title>Orphanet Journal of Rare Diseases</journal-title>
</journal-title-group>
<issn pub-type="epub">1750-1172</issn>
<publisher>
<publisher-name>BioMed Central</publisher-name>
<publisher-loc>London</publisher-loc>
</publisher>
</journal-meta>
<article-meta>
<article-id pub-id-type="pmid">27387831</article-id>
<article-id pub-id-type="pmc">4937550</article-id>
<article-id pub-id-type="publisher-id">463</article-id>
<article-id pub-id-type="doi">10.1186/s13023-016-0463-6</article-id>
<article-categories>
<subj-group subj-group-type="heading">
<subject>Erratum</subject>
</subj-group>
</article-categories>
<title-group>
<article-title>Erratum to: An exploratory randomised double-blind and placebo-controlled phase 2 study of a combination of baclofen, naltrexone and sorbitol (PXT3003) in patients with Charcot-Marie-Tooth disease type 1A</article-title>
</title-group>
<contrib-group>
<contrib contrib-type="author" equal-contrib="yes">
<name>
<surname>Attarian</surname>
<given-names>Shahram</given-names>
</name>
<xref ref-type="aff" rid="Aff1"></xref>
</contrib>
<contrib contrib-type="author">
<name>
<surname>Vallat</surname>
<given-names>Jean-Michel</given-names>
</name>
<xref ref-type="aff" rid="Aff3"></xref>
</contrib>
<contrib contrib-type="author">
<name>
<surname>Magy</surname>
<given-names>Laurent</given-names>
</name>
<xref ref-type="aff" rid="Aff3"></xref>
</contrib>
<contrib contrib-type="author">
<name>
<surname>Funalot</surname>
<given-names>Benoît</given-names>
</name>
<xref ref-type="aff" rid="Aff3"></xref>
</contrib>
<contrib contrib-type="author">
<name>
<surname>Gonnaud</surname>
<given-names>Pierre-Marie</given-names>
</name>
<xref ref-type="aff" rid="Aff4"></xref>
</contrib>
<contrib contrib-type="author">
<name>
<surname>Lacour</surname>
<given-names>Arnaud</given-names>
</name>
<xref ref-type="aff" rid="Aff5"></xref>
</contrib>
<contrib contrib-type="author">
<name>
<surname>Péréon</surname>
<given-names>Yann</given-names>
</name>
<xref ref-type="aff" rid="Aff6"></xref>
</contrib>
<contrib contrib-type="author">
<name>
<surname>Dubourg</surname>
<given-names>Odile</given-names>
</name>
<xref ref-type="aff" rid="Aff7"></xref>
</contrib>
<contrib contrib-type="author">
<name>
<surname>Pouget</surname>
<given-names>Jean</given-names>
</name>
<xref ref-type="aff" rid="Aff1"></xref>
</contrib>
<contrib contrib-type="author">
<name>
<surname>Micallef</surname>
<given-names>Joëlle</given-names>
</name>
<xref ref-type="aff" rid="Aff2"></xref>
</contrib>
<contrib contrib-type="author">
<name>
<surname>Franques</surname>
<given-names>Jérôme</given-names>
</name>
<xref ref-type="aff" rid="Aff1"></xref>
</contrib>
<contrib contrib-type="author">
<name>
<surname>Lefebvre</surname>
<given-names>Marie-Noëlle</given-names>
</name>
<xref ref-type="aff" rid="Aff2"></xref>
</contrib>
<contrib contrib-type="author">
<name>
<surname>Ghorab</surname>
<given-names>Karima</given-names>
</name>
<xref ref-type="aff" rid="Aff3"></xref>
</contrib>
<contrib contrib-type="author">
<name>
<surname>Al-Moussawi</surname>
<given-names>Mahmoud</given-names>
</name>
<xref ref-type="aff" rid="Aff4"></xref>
</contrib>
<contrib contrib-type="author">
<name>
<surname>Tiffreau</surname>
<given-names>Vincent</given-names>
</name>
<xref ref-type="aff" rid="Aff5"></xref>
</contrib>
<contrib contrib-type="author">
<name>
<surname>Preudhomme</surname>
<given-names>Marguerite</given-names>
</name>
<xref ref-type="aff" rid="Aff5"></xref>
</contrib>
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<name>
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<given-names>Laura</given-names>
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<given-names>Viviane</given-names>
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<given-names>Aude</given-names>
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<name>
<surname>Scart-Grès</surname>
<given-names>Catherine</given-names>
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<name>
<surname>Nabirotchkin</surname>
<given-names>Serguei</given-names>
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<surname>Guedj</surname>
<given-names>Mickael</given-names>
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<name>
<surname>Chumakov</surname>
<given-names>Ilya</given-names>
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<name>
<surname>Cohen</surname>
<given-names>Daniel</given-names>
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Centre de référence des maladies neuromusculaires et de la SLA, Pôle des neurosciences Cliniques, AP-HM et Aix Marseille Université, Marseille, France</aff>
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CIC-Centre de Pharmacologie Clinique et D’Evaluations Therapeutiques, AP-HM et Aix Marseille Université, Marseille, France</aff>
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<label></label>
CHU de Limoges - Hôpital Dupuytren, 2 Avenue Martin Luther King, 87042 Limoges, France</aff>
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CHU Lyon Sud, 165 Chemin du Grand Revoyet, 69495 Lyon, France</aff>
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CHRU de Lille - Hôpital Roger Salengro, rue Emile Laine, 59037 Lille, France</aff>
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CHU de Nantes - Hôtel Dieu, 1 place Alexis Ricordeau, 44093 Nantes, France</aff>
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CHU de Paris - Groupe Hospitalier Pitié-Salpétrière, 47-83 boulevard de l’Hôpital, 75013 Paris, France</aff>
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Admissions, 75017 Paris, France</aff>
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Faculty of Medicine, The University of Melbourne, Grattan St, Melbourne, VIC 3010 Australia</aff>
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<label></label>
Faculty of Economics, UCL Mons, Louvain, Belgium</aff>
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Carl M. Loeb University Professor Emeritus, Harvard University, Cambridge, MA 02138 USA</aff>
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Pharnext, 11, rue des Peupliers, 92130 Issy-Les-Moulineaux, Paris, France</aff>
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<pub-date pub-type="epub">
<day>7</day>
<month>7</month>
<year>2016</year>
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<pub-date pub-type="pmc-release">
<day>7</day>
<month>7</month>
<year>2016</year>
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<pub-date pub-type="collection">
<year>2016</year>
</pub-date>
<volume>11</volume>
<elocation-id>92</elocation-id>
<history>
<date date-type="received">
<day>16</day>
<month>5</month>
<year>2016</year>
</date>
<date date-type="accepted">
<day>16</day>
<month>5</month>
<year>2016</year>
</date>
</history>
<permissions>
<copyright-statement>© The Author(s). 2016</copyright-statement>
<license license-type="OpenAccess">
<license-p>
<bold>Open Access</bold>
This article is distributed under the terms of the Creative Commons Attribution 4.0 International License (
<ext-link ext-link-type="uri" xlink:href="http://creativecommons.org/licenses/by/4.0/">http://creativecommons.org/licenses/by/4.0/</ext-link>
), which permits unrestricted use, distribution, and reproduction in any medium, provided you give appropriate credit to the original author(s) and the source, provide a link to the Creative Commons license, and indicate if changes were made. The Creative Commons Public Domain Dedication waiver (
<ext-link ext-link-type="uri" xlink:href="http://creativecommons.org/publicdomain/zero/1.0/">http://creativecommons.org/publicdomain/zero/1.0/</ext-link>
) applies to the data made available in this article, unless otherwise stated.</license-p>
</license>
</permissions>
<related-article related-article-type="corrected-article" id="d30e69" ext-link-type="doi" xlink:href="10.1186/s13023-014-0199-0"></related-article>
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